Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: a retrospective case series analysis of nine sibships
Nouriya A. Al-Sannaa
◽
Luisa Bay
◽
Deborah S. Barbouth
◽
Youssef Benhayoun
◽
Cyril Goizet
◽
...
Brandon Bookstaver
◽
Moran
◽
Gerrald
Ather Mirza
◽
Terence Thomas
2019 ◽
Vol 114
(1)
◽
pp. S29-S29
Kazuki Yutsudo
◽
Akihito Tanaka
◽
Yuga Komaki
◽
Hiromichi Iwaya
◽
Shiho Arima
◽
...
2018 ◽
Vol 26
(5)
◽
pp. 1-7
Reema Kashiva
◽
Danish Memon
◽
Ram Agarwal
2011 ◽
Vol 6
(1)
◽
pp. 6283
◽
2015 ◽
Vol 70
(1)
◽
pp. 24-29
◽
J You
◽
Y Yue
◽
F Xing
◽
W Xia
◽
S Lai
◽
...
2018 ◽
Vol 20
(suppl_1)
◽
pp. i22-i22
Aditaya Kumar
◽
Athanasios Grivas
2015 ◽
Vol 51
(17)
◽
pp. 2609-2614
◽
Nadia Hindi
◽
Paolo G. Casali
◽
Carlo Morosi
◽
Antonella Messina
◽
Elena Palassini
◽
...
2018 ◽
Vol 38
(2)
◽
pp. 115-121
Afshin Teymoortash
◽
Stephan Hoch
◽
Daniel Weber
◽
Thomas Wilhelm
◽
Thomas Günzel