scholarly journals Long-Term Enzymatic and Phenotypic Correction in the Phenylketonuria Mouse Model by Adeno-Associated Virus Vector-Mediated Gene Transfer

2004 ◽  
Vol 56 (2) ◽  
pp. 278-284 ◽  
Author(s):  
Hyun-Jeong Oh ◽  
Eun-Sook Park ◽  
Seongman Kang ◽  
Inho Jo ◽  
Sung-Chul Jung
1996 ◽  
Vol 62 (6) ◽  
pp. 1669-1676 ◽  
Author(s):  
Michael G Kaplitt ◽  
Xiao Xiao ◽  
Richard J Samulski ◽  
Juan Li ◽  
Kaie Ojamaa ◽  
...  

1999 ◽  
Vol 380 (6) ◽  
Author(s):  
H. Büeler

AbstractAdeno-associated virus (AAV) is a defective, non-pathogenic human parvovirus that depends for growth on coinfection with a helper adenovirus or herpes virus. Recombinant adeno-associated viruses (rAAVs) have attracted considerable interest as vectors for gene therapy. In contrast to other gene delivery systems, rAAVs lack all viral genes and show long-term gene expression


Sign in / Sign up

Export Citation Format

Share Document