Short Report Of A Longterm Outcome Of A Patient With Lysosomal Acid Lipase Deficiency And First Results After Initiation Of Treatment With Sebelipase Alfa
Keyword(s):
2019 ◽
Vol 20
◽
pp. 100479
Keyword(s):
2020 ◽
Vol 99
(1)
◽
pp. 226-232
2019 ◽
Vol 68
(3)
◽
pp. 371-376
Keyword(s):
Keyword(s):
2014 ◽
Vol 61
(5)
◽
pp. 1135-1142
◽