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Compassionate Use of Simvastatin for a Patient with Juvenile Metachromatic Leukodystrophy
Neuropediatrics
◽
10.1055/s-0037-1602993
◽
2017
◽
Vol 48
(S 01)
◽
pp. S1-S45
Author(s):
A. Bley
◽
U. Löbel
◽
J. Denecke
Keyword(s):
Metachromatic Leukodystrophy
◽
Compassionate Use
Download Full-text
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10.1046/j.1365-2141.2000.02475.x
◽
2000
◽
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◽
pp. 1122-1129
◽
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◽
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◽
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◽
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◽
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◽
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◽
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A new score for assessing white matter changes in metachromatic leukodystrophy
Neuropediatrics
◽
10.1055/s-0029-1215737
◽
2008
◽
Vol 39
(05)
◽
Author(s):
M Wilke
◽
W Grodd
◽
C Kehrer
◽
I Krägeloh-Mann
Keyword(s):
White Matter
◽
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◽
White Matter Changes
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Metachromatic Leukodystrophy: spatial and temporal pattern of MRI changes and their association with motor deterioration
Neuropediatrics
◽
10.1055/s-0030-1265513
◽
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◽
Vol 41
(02)
◽
Author(s):
S Gröschel
◽
C Kehrer
◽
C i Dali
◽
M Wilke
◽
W Grodd
◽
...
Keyword(s):
Temporal Pattern
◽
Metachromatic Leukodystrophy
◽
Mri Changes
Download Full-text
Stem cell transplantation (SCT) in metachromatic leukodystrophy (MLD) - results from 9 patients
Neuropediatrics
◽
10.1055/s-0032-1307148
◽
2012
◽
Vol 43
(02)
◽
Author(s):
C Kehrer
◽
S Gröschel
◽
I Müller
◽
I Krägeloh-Mann
Keyword(s):
Stem Cell
◽
Stem Cell Transplantation
◽
Cell Transplantation
◽
Metachromatic Leukodystrophy
Download Full-text
FV 953. Parents’ Experiences during the Compassionate Use Program (Nusinersen) for Patients with Spinal Muscular Atrophy Type 1—A Qualitative Interview Study
10.1055/s-0038-1675931
◽
2018
◽
Author(s):
Thorsten Langer
◽
Petra Kiefer
◽
Astrid Pechmann
◽
Janbernd Kirschner
Keyword(s):
Spinal Muscular Atrophy
◽
Muscular Atrophy
◽
Qualitative Interview
◽
Interview Study
◽
Compassionate Use
◽
Spinal Muscular Atrophy Type
◽
Qualitative Interview Study
◽
Parents Experiences
Download Full-text
Influence of Age and Type of First Symptoms on Disease Progression in Metachromatic Leukodystrophy
10.1055/s-0039-1698236
◽
2019
◽
Author(s):
Saskia Elgün
◽
Christiane Kehrer
◽
Christa Raabe
◽
Judith Böhringer
◽
Andrea Bevot
◽
...
Keyword(s):
Disease Progression
◽
Metachromatic Leukodystrophy
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Metachromatic leukodystrophy – a case report of autistic features as a possible onset presentation
10.26226/morressier.5b68175db56e9b005965c4a5
◽
2018
◽
Author(s):
Roxana Daniela Neacsu
◽
Anca Cerlinca
◽
Ilinca Mihailescu
Keyword(s):
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◽
Metachromatic Leukodystrophy
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J-Valve Compassionate Use
Case Medical Research
◽
10.31525/ct1-nct03876964
◽
2019
◽
Author(s):
Keyword(s):
Compassionate Use
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Compassionate Use Re-Infusion of ATLCAR.CD30
Case Medical Research
◽
10.31525/ct1-nct03914885
◽
2019
◽
Author(s):
Keyword(s):
Compassionate Use
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Smoke and Mirrors: Barriers to Compassionate-Use of Marijuana in Texas
SSRN Electronic Journal
◽
10.2139/ssrn.2893809
◽
2016
◽
Author(s):
Cielo Fortin-Camacho
Keyword(s):
Compassionate Use
Download Full-text
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