Faculty Opinions recommendation of Eplerenone for early cardiomyopathy in Duchenne muscular dystrophy: a randomised, double-blind, placebo-controlled trial.

Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature ◽

10.3410/f.725296619.793535821 ◽

2017 ◽

Author(s):

WH Wilson Tang

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Controlled Trial ◽

Double Blind ◽

Double Blind Placebo

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Treatment of Duchenne muscular dystrophy with cyclosporin A – A randomized, double-blind, placebo controlled trial

Neuropediatrics ◽

10.1055/s-0029-1215757 ◽

2008 ◽

Vol 39 (05) ◽

Author(s):

J Kirschner ◽

J Schessl ◽

G Ihorst ◽

R Korinthenberg

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Cyclosporin A ◽

Controlled Trial ◽

Double Blind ◽

Double Blind Placebo

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Effect and safety of treatment with ACE-inhibitor Enalapril and β-blocker metoprolol on the onset of left ventricular dysfunction in Duchenne muscular dystrophy - a randomized, double-blind, placebo-controlled trial

Orphanet Journal of Rare Diseases ◽

10.1186/s13023-019-1066-9 ◽

2019 ◽

Vol 14 (1) ◽

Author(s):

Sven Dittrich ◽

◽

Erika Graf ◽

Regina Trollmann ◽

Ulrich Neudorf ◽

...

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Left Ventricular Dysfunction ◽

Ace Inhibitor ◽

Ventricular Dysfunction ◽

Controlled Trial ◽

Left Ventricular ◽

Double Blind ◽

Double Blind Placebo ◽

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Eplerenone for early cardiomyopathy in Duchenne muscular dystrophy: a randomised, double-blind, placebo-controlled trial

The Lancet Neurology ◽

10.1016/s1474-4422(14)70318-7 ◽

2015 ◽

Vol 14 (2) ◽

pp. 153-161 ◽

Author(s):

Subha V Raman ◽

Kan N Hor ◽

Wojciech Mazur ◽

Nancy J Halnon ◽

John T Kissel ◽

...

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Controlled Trial ◽

Double Blind ◽

Double Blind Placebo

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P.11.18 Design of a confirmatory phase 3, multicenter, randomized, double-blind, placebo-controlled study of ataluren in patients with nonsense mutation Duchenne muscular dystrophy

Neuromuscular Disorders ◽

10.1016/j.nmd.2013.06.579 ◽

2013 ◽

Vol 23 (9-10) ◽

pp. 804

Author(s):

J. Barth ◽

A. Reha ◽

R. Spiegel ◽

G.L. Elfring ◽

M. Husain ◽

...

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Nonsense Mutation ◽

Controlled Study ◽

Phase 3 ◽

Double Blind ◽

Double Blind Placebo ◽

Confirmatory Phase

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T.O.3 SNT-MC17/idebenone in Duchenne muscular dystrophy: long-term blinded controlled preclinical study in the mdx mouse followed by a 12 month double-blind randomized controlled trial in humans

Neuromuscular Disorders ◽

10.1016/j.nmd.2008.06.378 ◽

2008 ◽

Vol 18 (9-10) ◽

pp. 832 ◽

Author(s):

G.M. Buyse ◽

N. Goemans ◽

G. Van der Mieren ◽

M. Erb ◽

J. D’hooge ◽

...

Keyword(s):

Randomized Controlled Trial ◽

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Controlled Trial ◽

Preclinical Study ◽

Mdx Mouse ◽

Double Blind ◽

Randomized Controlled

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Effect and Safety of Treatment with ACE-Inhibitor Enalapril and β-Blocker Metoprolol on the Onset of Left Ventricular Dysfunction in Duchenne Muscular Dystrophy: Results from a Six Years, Double-blind, Randomized Placebo-controlled Trial

10.1055/s-0038-1628322 ◽

2018 ◽

Author(s):

S. Dittrich ◽

E. Graf ◽

U. Neudorf ◽

A. Heilmann ◽

U. Schara ◽

...

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Left Ventricular Dysfunction ◽

Ace Inhibitor ◽

Ventricular Dysfunction ◽

Controlled Trial ◽

Left Ventricular ◽

Double Blind ◽

Download Full-text

Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

10.1016/s0140-6736(17)31611-2 ◽

2017 ◽

Vol 390 (10101) ◽

pp. 1489-1498 ◽

Author(s):

Craig M McDonald ◽

Craig Campbell ◽

Ricardo Erazo Torricelli ◽

Richard S Finkel ◽

Kevin M Flanigan ◽

...

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Nonsense Mutation ◽

Phase 3 ◽

Double Blind ◽

Double Blind Placebo

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Safety, tolerability, and pharmacokinetics of casimersen in patients with Duchenne muscular dystrophy amenable to exon 45 skipping: A randomized, double‐blind, placebo‐controlled, dose‐titration trial

Muscle & Nerve ◽

10.1002/mus.27347 ◽

2021 ◽

Author(s):

Kathryn R. Wagner ◽

Nancy L. Kuntz ◽

Erica Koenig ◽

Lilly East ◽

Sameer Upadhyay ◽

...

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Dose Titration ◽

Double Blind ◽

Double Blind Placebo

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Faculty Opinions recommendation of Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial.

Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature ◽

10.3410/f.727824728.793536094 ◽

2017 ◽

Author(s):

Manoj Menezes

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Nonsense Mutation ◽

Phase 3 ◽

Double Blind ◽

Double Blind Placebo

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A double-blind randomised multi-centre, placebo-controlled trial of combined angiotensin converting enzyme-inhibitor and beta-blocker therapy in preventing the development of cardiomyopathy in genetically characterised males with Duchenne Muscular Dystrophy without echo-detectable left ventricular dysfunction

http://isrctn.org/> ◽

10.1186/isrctn50395346 ◽

2012 ◽

Author(s):

John Bourke

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Angiotensin Converting Enzyme ◽

Ventricular Dysfunction ◽

Enzyme Inhibitor ◽

Controlled Trial ◽

Left Ventricular ◽

Converting Enzyme ◽

Double Blind ◽

Blocker Therapy

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