scholarly journals Enzyme Replacement Therapy in Mucopolysaccharidosis II Patients Under 1 Year of Age

2014 ◽  
pp. 99-113 ◽  
Author(s):  
Christina Lampe ◽  
Andrea Atherton ◽  
Barbara K. Burton ◽  
Maria Descartes ◽  
Roberto Giugliani ◽  
...  



2013 ◽  
Vol 30 (7) ◽  
pp. 727-732 ◽  
Author(s):  
Nicola Volpi ◽  
Lucia Zampini ◽  
Francesca Maccari ◽  
Lucia Santoro ◽  
Fabio Galeotti ◽  
...  


2007 ◽  
Vol 92 (4) ◽  
pp. 18 ◽  
Author(s):  
Christine Eng ◽  
J. Muenzer ◽  
E. Wraith ◽  
M. Beck ◽  
R. Giugliani ◽  
...  


2014 ◽  
Vol 30 (4) ◽  
pp. 189-193 ◽  
Author(s):  
G. W. Negretto ◽  
M. Deon ◽  
G. B. Biancini ◽  
M. G. Burin ◽  
R. Giugliani ◽  
...  




2020 ◽  
Vol 129 (2) ◽  
pp. 98-105 ◽  
Author(s):  
A. Broomfield ◽  
J. Davison ◽  
J. Roberts ◽  
C. Stewart ◽  
P. Hensman ◽  
...  






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