scholarly journals PRO62 SPINAL MUSCULAR ATROPHY: DEVELOPMENT OF NATURAL HISTORY MODELS FOR DISEASE SUBTYPES

2020 ◽  
Vol 23 ◽  
pp. S339
Author(s):  
N. Paracha ◽  
K. Gorni ◽  
P. Hudson
Author(s):  
Mélanie Annoussamy ◽  
Andreea M. Seferian ◽  
Aurore Daron ◽  
Yann Péréon ◽  
Claude Cances ◽  
...  

2019 ◽  
Vol 29 ◽  
pp. S132
Author(s):  
J. Exposito ◽  
D. Natera-de Benito ◽  
L. Carrera ◽  
A. Frongia ◽  
M. Alarcón ◽  
...  

2020 ◽  
Vol 15 (1) ◽  
Author(s):  
Eugenio Mercuri ◽  
Simona Lucibello ◽  
Marco Perulli ◽  
Giorgia Coratti ◽  
Roberto de Sanctis ◽  
...  

2015 ◽  
Vol 25 ◽  
pp. S195
Author(s):  
M. Annoussamy ◽  
A. Chabanon ◽  
A. Phelep ◽  
J.Y. Hogrel ◽  
P. Carlier ◽  
...  

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