487. Liver-Targeted Gene Therapy in Glycogen Storage Disease Type Ia (GSD-Ia) Requires Widespread, Regulated Glucose-6-phosphatase
Dwight D. Koeberl
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Lopamudra Banerjee
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Andrew Bird
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Baodong Sun
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Y.T. Chen
2017 ◽
Vol 26
(10)
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pp. 1890-1899
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Goo-Young Kim
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Joon Hyun Kwon
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Jun-Ho Cho
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Lisa Zhang
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Brian C. Mansfield
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...
2012 ◽
Vol 56
(5)
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pp. 1719-1729
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Young Mok Lee
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Hyun Sik Jun
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Chi-Jiunn Pan
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Su Ru Lin
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Lane H. Wilson
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...
2007 ◽
Vol 14
(3)
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pp. 281-281
D D Koeberl
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B D Sun
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T V Damodaran
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T Brown
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D S Millington
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...
2019 ◽
Vol 42
(3)
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pp. 459-469
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Jun-Ho Cho
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Young Mok Lee
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Matthew F. Starost
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Brian C. Mansfield
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Janice Y. Chou
2002 ◽
Vol 5
(5)
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pp. S342
2008 ◽
Vol 93
(2)
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pp. 38-39
Baodong Sun
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Stephen Hauschka
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Andrew Bird
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Richard Auten
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Dwight Koeberl
2007 ◽
Vol 15
(11)
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pp. 2051
Dwight D Koeberl
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Baodong Sun
◽
Andrew Bird
◽
Yuan-Tsong Chen
◽
Kazuhiro Oka
◽
...
2010 ◽
Vol 18
(6)
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pp. 1076-1084
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Wai Han Yiu
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Young Mok Lee
◽
Wen-Tao Peng
◽
Chi-Jiunn Pan
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Paul A Mead
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...
2012 ◽
Vol 56
(5)
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pp. 1593-1595
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2018 ◽
Vol 41
(6)
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pp. 913-914
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Elizabeth D. Brooks
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Priya S. Kishnani
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Dwight D. Koeberl