124. Therapeutic Correction of an LCA-Causing Splice Defect in the CEP290 Gene by CRISPR/Cas-Mediated Gene Editing
2016 ◽
Vol 24
◽
pp. S51-S52
◽
Morgan L. Maeder
◽
Rina Mepani
◽
Sebastian Gloskowski
◽
Maxwell Skor
◽
McKensie Collins
◽
...
2017 ◽
Vol 236
(3150)
◽
pp. 17
2018 ◽
Vol 20
(6)
◽
pp. 82
Hongbing Han
◽
Kabin Xie
◽
Gang Cao
◽
Jianhui Tian
◽
Dong Wang
2019 ◽
Vol 68
(Supplement 1)
◽
pp. 478-P
KYOUNGMIN PARK
◽
QIAN LI
◽
HAIYAN WANG
◽
RONALD ST-LOUIS
◽
HISASHI YOKOMIZO
◽
...
Kimberly Coughlan
◽
Rajanikanth Maganti
◽
Andrea Frassetto
◽
Christine DeAntonis
◽
Meredith Wolfrom
◽
...