687. Therapeutic Correction of an LCA-Causing Splice Defect in the CEP290 Gene by CRISPR/Cas-Mediated Genome Editing
2015 ◽
Vol 23
◽
pp. S273-S274
◽
Morgan L. Maeder
◽
Shen Shen
◽
Erin R. Burnight
◽
Sebastian Gloskowski
◽
Rina Mepani
◽
...
2017 ◽
Vol 6
(3)
◽
pp. 162-162
Liane Kaufmann
◽
Michael von Aster
M Keller
◽
J Dalla-Riva
◽
A Kurbasic
◽
M Al-Majdoub
◽
P Spegel
◽
...
T. V. Dimitireva
◽
◽
D. A. Reshetov
◽
V. E. Zhernovkov
◽
D. E. Vlodavets
◽
...
2019 ◽
Vol 11
(4)
◽
pp. 422-429
N.A. Rozhnova
◽
G.A. Gerashchenkov
◽
A.V. Chemeris
2020 ◽
Vol 86
(4)
◽
pp. 264
Michel Sadelain
◽
Eirini Papapetrou