scholarly journals 494. Hematopoietic Stem Cell Gene Therapy for Cystinosis

2013 ◽  
Vol 21 ◽  
pp. S190-S191
2021 ◽  
Vol 132 (2) ◽  
pp. S107
Author(s):  
Niek P. van Til ◽  
Yildirim Dogan ◽  
Cecilia Barese ◽  
Zeenath Unnisa ◽  
Swaroopa Guda ◽  
...  

Gene Therapy ◽  
1999 ◽  
Vol 6 (6) ◽  
pp. 1038-1044 ◽  
Author(s):  
K M Matsuda ◽  
A Kume ◽  
Y Ueda ◽  
M Urabe ◽  
M Hasegawa ◽  
...  

2017 ◽  
Vol 28 (10) ◽  
pp. 782-799 ◽  
Author(s):  
Saskia Kohlscheen ◽  
Halvard Bonig ◽  
Ute Modlich

Cell Therapy ◽  
2000 ◽  
pp. 159-169
Author(s):  
Yutaka Hanazono ◽  
Cynthia E. Dunbar ◽  
Robert E. Donahue ◽  
Ikunoshin Kato ◽  
Yasuji Ueda ◽  
...  

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