scholarly journals Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency

2021 ◽  
Author(s):  
Donald B. Kohn ◽  
Claire Booth ◽  
Kit L. Shaw ◽  
Jinhua Xu-Bayford ◽  
Elizabeth Garabedian ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Adenosine Deaminase ◽  
Ex Vivo ◽  
Adenosine Deaminase Deficiency ◽  
Lentiviral Gene Therapy

Gene therapy for adenosine deaminase deficiency

1995 ◽  
Vol 51 (1) ◽  
pp. 72-81 ◽  
Author(s):  
P M Hoogerbrugge ◽  
V W v Beusechem ◽  
L C M Kaptein ◽  
M P W Einerhand ◽  
D Valerio
Keyword(s):  
Gene Therapy ◽  
Adenosine Deaminase ◽  
Adenosine Deaminase Deficiency

Phase I study protocol for ex-vivo lentiviral gene therapy for the inherited skin disease, Netherton Syndrome

2013 ◽  
pp. 150127063140004
Author(s):  
Wei-Li Di ◽  
Jemima E Mellerio ◽  
Catina Bernadis ◽  
John Harper ◽  
Alya Abdul-Wahab ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Phase I ◽  
Study Protocol ◽  
Skin Disease ◽  
Phase I Study ◽  
Ex Vivo ◽  
Netherton Syndrome ◽  
Lentiviral Gene Therapy

scholarly journals Outcomes in Two Japanese Adenosine Deaminase-Deficiency Patients Treated by Stem Cell Gene Therapy with No Cytoreductive Conditioning

2015 ◽  
Vol 35 (4) ◽  
pp. 384-398 ◽  
Author(s):  
Makoto Otsu ◽  
Masafumi Yamada ◽  
Satoru Nakajima ◽  
Miyuki Kida ◽  
Yoshihiro Maeyama ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Adenosine Deaminase ◽  
Adenosine Deaminase Deficiency ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy
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