Successful Use of Eltrombopag in a Child With Hurler Syndrome After Haploidentical Hematopoietic Stem Cell Transplantation

Journal of Pediatric Hematology/Oncology ◽

10.1097/mph.0000000000000451 ◽

2016 ◽

Vol 38 (2) ◽

pp. 163-164 ◽

Author(s):

Rahul Naithani ◽

Mansi Sachdev ◽

Rajiv Uttam

Keyword(s):

Stem Cell ◽

Hematopoietic Stem Cell Transplantation ◽

Stem Cell Transplantation ◽

Cell Transplantation ◽

Hematopoietic Stem Cell ◽

Hurler Syndrome ◽

Hematopoietic Stem

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Combination of enzyme replacement and hematopoietic stem cell transplantation as therapy for Hurler syndrome

Bone Marrow Transplantation ◽

10.1038/sj.bmt.1705934 ◽

2007 ◽

Vol 41 (6) ◽

pp. 531-535 ◽

Author(s):

J Tolar ◽

S S Grewal ◽

K J Bjoraker ◽

C B Whitley ◽

E G Shapiro ◽

...

Keyword(s):

Stem Cell ◽

Hematopoietic Stem Cell Transplantation ◽

Stem Cell Transplantation ◽

Cell Transplantation ◽

Hematopoietic Stem Cell ◽

Hurler Syndrome ◽

Hematopoietic Stem ◽

Enzyme Replacement

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Genu Valgum Deformity in Hurler Syndrome After Hematopoietic Stem Cell Transplantation: Correction by Surgical Intervention

Journal of Pediatric Orthopaedics ◽

10.1097/01241398-199903000-00026 ◽

1999 ◽

Vol 19 (2) ◽

pp. 270-274 ◽

Author(s):

Ebenezer Odunusi ◽

Charles Peters ◽

William Krivit ◽

James Ogilvie

Keyword(s):

Stem Cell ◽

Hematopoietic Stem Cell Transplantation ◽

Stem Cell Transplantation ◽

Cell Transplantation ◽

Hematopoietic Stem Cell ◽

Surgical Intervention ◽

Genu Valgum ◽

Hurler Syndrome ◽

Hematopoietic Stem

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Hematopoietic stem cell transplantation in patients with Hurler syndrome – myeloablative conditioning efficiency

Russian Journal of Pediatric Hematology and Oncology ◽

10.17650/2311-1267-2015-2-3-46-50 ◽

2015 ◽

Vol 2 (3) ◽

pp. 46-50 ◽

Author(s):

K. I. Kirgizov ◽

E. A. Pristanskova ◽

N. V. Sidorova ◽

V. V. Konstantinova ◽

B. B. Purbueva ◽

...

Keyword(s):

Stem Cell ◽

Hematopoietic Stem Cell Transplantation ◽

Stem Cell Transplantation ◽

Cell Transplantation ◽

Hematopoietic Stem Cell ◽

Hurler Syndrome ◽

Myeloablative Conditioning ◽

Hematopoietic Stem

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97 Growth and the use of growth hormone in patients with Hurler syndrome following hematopoietic stem cell transplantation

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2007.08.102 ◽

2007 ◽

Vol 92 (4) ◽

pp. 31

Author(s):

Lynda Polgreen ◽

Melissa Plog ◽

Paul Orchard ◽

Bradley Miller ◽

Anna Petryk

Keyword(s):

Growth Hormone ◽

Stem Cell ◽

Hematopoietic Stem Cell Transplantation ◽

Stem Cell Transplantation ◽

Cell Transplantation ◽

Hematopoietic Stem Cell ◽

Hurler Syndrome ◽

Hematopoietic Stem

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Dried Blood Spot Analysis: An Easy and Reliable Tool to Monitor the Biochemical Effect of Hematopoietic Stem Cell Transplantation in Hurler Syndrome Patients

Biology of Blood and Marrow Transplantation ◽

10.1016/j.bbmt.2010.01.006 ◽

2010 ◽

Vol 16 (5) ◽

pp. 701-704 ◽

Author(s):

Mieke Aldenhoven ◽

Tom J. de Koning ◽

Frans W. Verheijen ◽

Berthil H. Prinsen ◽

Frits A. Wijburg ◽

...

Keyword(s):

Stem Cell ◽

Hematopoietic Stem Cell Transplantation ◽

Stem Cell Transplantation ◽

Cell Transplantation ◽

Hematopoietic Stem Cell ◽

Hurler Syndrome ◽

Biochemical Effect ◽

Hematopoietic Stem ◽

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Changes in the incidence, patterns and outcomes of graft failure following hematopoietic stem cell transplantation for Hurler syndrome

Bone Marrow Transplantation ◽

10.1038/bmt.2017.5 ◽

2017 ◽

Vol 52 (6) ◽

pp. 846-853 ◽

Author(s):

S H Lum ◽

W P Miller ◽

S Jones ◽

K Poulton ◽

W Ogden ◽

...

Keyword(s):

Stem Cell ◽

Hematopoietic Stem Cell Transplantation ◽

Stem Cell Transplantation ◽

Cell Transplantation ◽

Hematopoietic Stem Cell ◽

Graft Failure ◽

Hurler Syndrome ◽

Hematopoietic Stem

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Long-term follow up of post-hematopoietic stem cell transplantation for Hurler syndrome: Clinical biochemical and pathological improvements

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2014.12.265 ◽

2015 ◽

Vol 114 (2) ◽

pp. S116

Author(s):

Shunji Tomatsu ◽

Eriko Yasuda ◽

Kristen Ruhnke ◽

Tsutomu Shimada ◽

Robert W. Mason ◽

...

Keyword(s):

Stem Cell ◽

Hematopoietic Stem Cell Transplantation ◽

Stem Cell Transplantation ◽

Cell Transplantation ◽

Hematopoietic Stem Cell ◽

Hurler Syndrome ◽

Hematopoietic Stem ◽

Long Term Follow Up

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Allogenic hematopoietic stem cell transplantation for patients with Hurler syndrome: Long-time follow-up and late effects estimation

European Journal of Paediatric Neurology ◽

10.1016/j.ejpn.2017.04.1011 ◽

2017 ◽

Vol 21 ◽

pp. e127

Author(s):

K. Kirgizov ◽

A. Borovkova ◽

T. Bykova ◽

O. Slesarchuk ◽

E. Pristanskova ◽

...

Keyword(s):

Stem Cell ◽

Hematopoietic Stem Cell Transplantation ◽

Stem Cell Transplantation ◽

Cell Transplantation ◽

Hematopoietic Stem Cell ◽

Late Effects ◽

Hurler Syndrome ◽

Hematopoietic Stem ◽

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HURLER SYNDROME: 15 YEARS OF HEMATOPOIETIC STEM CELL TRANSPLANTATION WITH HURLER SYNDROME AT THE RUSSIAN CHILDREN’S CLINICAL HOSPITAL

PEDIATRIA Journal named after G N SPERANSKY ◽

10.24110/0031-403x-2019-98-6-188-194 ◽

2019 ◽

Vol 98 (6) ◽

pp. 188-194

Author(s):

E.A. Pristanskova ◽

◽

K.I. Kirgizov ◽

S.V. Mikhaylova ◽

E.K. Donyush ◽

...

Keyword(s):

Stem Cell ◽

Hematopoietic Stem Cell Transplantation ◽

Stem Cell Transplantation ◽

Cell Transplantation ◽

Hematopoietic Stem Cell ◽

Hurler Syndrome ◽

Hematopoietic Stem ◽

Clinical Hospital

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Hearing outcomes following hematopoietic stem cell transplantation in Hurler syndrome

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2016.11.289 ◽

2017 ◽

Vol 120 (1-2) ◽

pp. S112-S113

Author(s):

Hannah Qualls ◽

Madeline Heck ◽

Abby Meyer

Keyword(s):

Stem Cell ◽

Hematopoietic Stem Cell Transplantation ◽

Stem Cell Transplantation ◽

Cell Transplantation ◽

Hematopoietic Stem Cell ◽

Hurler Syndrome ◽

Hematopoietic Stem ◽

Hearing Outcomes

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