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Faculty Opinions recommendation of Correction of murine Rag2 severe combined immunodeficiency by lentiviral gene therapy using a codon-optimized RAG2 therapeutic transgene.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.722644269.793515036
◽
2016
◽
Author(s):
Fabio Candotti
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Lentiviral Gene Therapy
Download Full-text
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Cited By
References
254. Correction of RAG2 Severe Combined Immunodeficiency by Lentiviral Gene Therapy Requires Strong Expression of RAG2
Molecular Therapy
◽
10.1016/s1525-0016(16)36826-5
◽
2011
◽
Vol 19
◽
pp. S99
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Strong Expression
◽
Lentiviral Gene Therapy
Download Full-text
617. Lentiviral Gene Therapy of RAG1 Severe Combined Immunodeficiency: Risks and Implications for Treatment
Molecular Therapy
◽
10.1016/s1525-0016(16)38058-3
◽
2010
◽
Vol 18
◽
pp. S240
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Lentiviral Gene Therapy
Download Full-text
230. Correction of Immunity in Murine Rag2 Severe Combined Immunodeficiency by Lentiviral Gene Therapy Using a Codon-Optimized RAG2 Therapeutic Transgene
Molecular Therapy
◽
10.1016/s1525-0016(16)36034-8
◽
2012
◽
Vol 20
◽
pp. S90-S91
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Lentiviral Gene Therapy
Download Full-text
Correction of Murine Rag2 Severe Combined Immunodeficiency by Lentiviral Gene Therapy Using a Codon-optimized RAG2 Therapeutic Transgene
Molecular Therapy
◽
10.1038/mt.2012.110
◽
2012
◽
Vol 20
(10)
◽
pp. 1968-1980
◽
Cited By ~ 37
Author(s):
Niek P van Til
◽
Helen de Boer
◽
Nomusa Mashamba
◽
Agnieszka Wabik
◽
Marshall Huston
◽
...
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Lentiviral Gene Therapy
Download Full-text
243. Pre-Clinical Development of Lentiviral Gene Therapy for X-Linked Severe Combined Immunodeficiency
Molecular Therapy
◽
10.1016/s1525-0016(16)33848-5
◽
2015
◽
Vol 23
◽
pp. S95
Author(s):
Valentina Poletti
◽
Sabine Charrier
◽
Samia Martin
◽
Arianna Moiani
◽
Céline Sagrère
◽
...
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Clinical Development
◽
Combined Immunodeficiency
◽
Lentiviral Gene Therapy
Download Full-text
661. Lentiviral Gene Therapy of RAG Severe Combined Immunodeficiency
Molecular Therapy
◽
10.1016/s1525-0016(16)34996-6
◽
2013
◽
Vol 21
◽
pp. S252
◽
Cited By ~ 1
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Lentiviral Gene Therapy
Download Full-text
415. Development of a Lentiviral Gene Therapy for Adenosine Deaminase-Deficient Severe Combined Immunodeficiency (ADA-SCID)
Molecular Therapy
◽
10.1016/s1525-0016(16)36219-0
◽
2012
◽
Vol 20
◽
pp. S162
Keyword(s):
Gene Therapy
◽
Adenosine Deaminase
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Lentiviral Gene Therapy
Download Full-text
Faculty Opinions recommendation of Recombination-activating gene 1 (Rag1)-deficient mice with severe combined immunodeficiency treated with lentiviral gene therapy demonstrate autoimmune Omenn-like syndrome.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.718206925.793515037
◽
2016
◽
Author(s):
Fabio Candotti
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Recombination Activating Gene
◽
Lentiviral Gene Therapy
◽
Deficient Mice
Download Full-text
Recombination-activating gene 1 (Rag1)–deficient mice with severe combined immunodeficiency treated with lentiviral gene therapy demonstrate autoimmune Omenn-like syndrome
Journal of Allergy and Clinical Immunology
◽
10.1016/j.jaci.2013.10.009
◽
2014
◽
Vol 133
(4)
◽
pp. 1116-1123
◽
Cited By ~ 35
Author(s):
Niek P. van Til
◽
Roya Sarwari
◽
Trudi P. Visser
◽
Julia Hauer
◽
Chantal Lagresle-Peyrou
◽
...
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Recombination Activating Gene
◽
Lentiviral Gene Therapy
◽
Deficient Mice
Download Full-text
Faculty Opinions recommendation of Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.1005837.70356
◽
2002
◽
Author(s):
Seppo Yla-Herttuala
Keyword(s):
Gene Therapy
◽
Ex Vivo
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Ex Vivo Gene Therapy
Download Full-text
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