P06—Enzyme Replacement Therapy with Agalsidase Beta for Fabry Disease: Importance of the Doses—A Case Report

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

Uneventful pregnancy outcome after enzyme replacement therapy with agalsidase beta in a heterozygous female with Fabry disease: A case report

European Journal of Medical Genetics ◽

10.1016/j.ejmg.2009.12.004 ◽

2010 ◽

Vol 53 (2) ◽

pp. 111-112 ◽

Cited By ~ 8

Author(s):

Dominique P. Germain ◽

Patrick Bruneval ◽

Thi-Chien Tran ◽

Pierre Balouet ◽

Bernard Richalet ◽

...

Keyword(s):

Case Report ◽

Fabry Disease ◽

Replacement Therapy ◽

Pregnancy Outcome ◽

Agalsidase Beta ◽

Heterozygous Female ◽

Enzyme Replacement ◽

Uneventful Pregnancy

Successful Management of Enzyme Replacement Therapy in Related Fabry Disease Patients with Severe Adverse Events by Switching from Agalsidase Beta (Fabrazyme®) to Agalsidase Alfa (Replagal®)

10.1007/8904_2014_304 ◽

2014 ◽

Cited By ~ 1

Author(s):

Kazuya Tsuboi ◽

Hiroshi Yamamoto ◽

Fuji Somura ◽

Hiromi Goto

Keyword(s):

Adverse Events ◽

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

Successful Management ◽

Enzyme Replacement ◽

Agalsidase Alfa ◽

Severe Adverse Events

Burden of Fabry disease in young patients (≤30 years of age) who were initiated on enzyme replacement therapy with agalsidase beta: a Fabry Registry analysis

10.1016/j.ymgme.2016.11.151 ◽

2017 ◽

Vol 120 (1-2) ◽

pp. S65-S66

Author(s):

Robert J. Hopkin ◽

Eva Brand ◽

Ulla F. Rasmussen ◽

Dominique P. Germain ◽

Nathalie Guffon ◽

...

Keyword(s):

Fabry Disease ◽

Replacement Therapy ◽

Young Patients ◽

Agalsidase Beta ◽

Enzyme Replacement ◽

Registry Analysis

Enzyme replacement therapy in Fabry disease: Comparison of agalsidase alfa and agalsidase beta

10.1016/j.ymgme.2008.07.002 ◽

2008 ◽

Vol 95 (1-2) ◽

pp. 114-115 ◽

Cited By ~ 15

Author(s):

Atul Mehta ◽

Michael Beck ◽

Christoph Kampmann ◽

Andrea Frustaci ◽

Dominique P. Germain ◽

...

Keyword(s):

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

Enzyme Replacement ◽

Ten-year outcome of enzyme replacement therapy with agalsidase beta in patients with Fabry disease

Journal of Medical Genetics ◽

10.1136/jmedgenet-2014-102797 ◽

2015 ◽

Vol 52 (5) ◽

pp. 353-358 ◽

Cited By ~ 151

Author(s):

Dominique P Germain ◽

Joel Charrow ◽

Robert J Desnick ◽

Nathalie Guffon ◽

Judy Kempf ◽

...

Keyword(s):

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

An open-label, switchover trial to assess the safety and efficacy of agalsidase beta in patients with Fabry disease treated with agalsidase alfa enzyme replacement therapy

10.1016/j.ymgme.2013.12.217 ◽

2014 ◽

Vol 111 (2) ◽

pp. S90

Author(s):

Sarah Richards ◽

Dawn Laney ◽

Muhammad A. Pervaiz ◽

Suma Shankar

Keyword(s):

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

Open Label ◽

Safety And Efficacy ◽

Enzyme Replacement ◽

Fabry disease and enzyme replacement therapy: 10years of experience with agalsidase beta

10.1016/j.ymgme.2013.12.210 ◽

2014 ◽

Vol 111 (2) ◽

pp. S87

Author(s):

Juan Politei ◽

Andrea Schenone ◽

Gustavo Cabrera ◽

Hernan Amartino ◽

Marina Szlago

Keyword(s):

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

Clinical observations on enzyme replacement therapy in patients with Fabry disease and the switch from agalsidase beta to agalsidase alfa

Journal of the Chinese Medical Association ◽

10.1016/j.jcma.2013.11.006 ◽

2014 ◽

Vol 77 (4) ◽

pp. 190-197 ◽

Cited By ~ 7

Author(s):

Hsiang-Yu Lin ◽

Yu-Hsiu Huang ◽

Hsuan-Chieh Liao ◽

Hao-Chuan Liu ◽

Ting-Rong Hsu ◽

...

Keyword(s):

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

Enzyme Replacement ◽

Clinical Observations ◽

Enzyme replacement therapy in a patient with Fabry disease and the development of IgE antibodies against agalsidase beta but not agalsidase alpha

Journal of Inherited Metabolic Disease ◽

10.1007/s10545-010-9136-0 ◽

2010 ◽

Vol 33 (S3) ◽

pp. 249-252 ◽

Cited By ~ 14

Author(s):

Akemi Tanaka ◽

Taisuke Takeda ◽

Takao Hoshina ◽

Kazuyoshi Fukai ◽

Tsunekazu Yamano

Keyword(s):

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

Ige Antibodies ◽

Prospective Results of Switching Enzyme Replacement Therapy from Agalsidase beta to Agalsidase alfa in the Canadian Fabry Disease Initiative Study

10.1016/j.ymgme.2011.11.174 ◽

2012 ◽

Vol 105 (2) ◽

pp. S64-S65

Author(s):

Michael West ◽

Daniel Bichet ◽

Robin Casey ◽

Joe Clarke ◽

Sandra Sirrs ◽

...

Keyword(s):

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

Enzyme Replacement ◽