Burden of Fabry disease in young patients (≤30 years of age) who were initiated on enzyme replacement therapy with agalsidase beta: a Fabry Registry analysis

2017 ◽  
Vol 120 (1-2) ◽  
pp. S65-S66
Author(s):  
Robert J. Hopkin ◽  
Eva Brand ◽  
Ulla F. Rasmussen ◽  
Dominique P. Germain ◽  
Nathalie Guffon ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Fabry Disease ◽  
Replacement Therapy ◽  
Young Patients ◽  
Agalsidase Beta ◽  
Enzyme Replacement ◽  
Registry Analysis

Enzyme replacement therapy in Fabry disease: Comparison of agalsidase alfa and agalsidase beta

2008 ◽  
Vol 95 (1-2) ◽  
pp. 114-115 ◽  
Author(s):  
Atul Mehta ◽  
Michael Beck ◽  
Christoph Kampmann ◽  
Andrea Frustaci ◽  
Dominique P. Germain ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Fabry Disease ◽  
Replacement Therapy ◽  
Agalsidase Beta ◽  
Enzyme Replacement ◽  
Agalsidase Alfa

scholarly journals Ten-year outcome of enzyme replacement therapy with agalsidase beta in patients with Fabry disease

2015 ◽  
Vol 52 (5) ◽  
pp. 353-358 ◽  
Author(s):  
Dominique P Germain ◽  
Joel Charrow ◽  
Robert J Desnick ◽  
Nathalie Guffon ◽  
Judy Kempf ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Fabry Disease ◽  
Replacement Therapy ◽  
Agalsidase Beta ◽  
Enzyme Replacement

Fabry disease and enzyme replacement therapy: 10years of experience with agalsidase beta

2014 ◽  
Vol 111 (2) ◽  
pp. S87
Author(s):  
Juan Politei ◽  
Andrea Schenone ◽  
Gustavo Cabrera ◽  
Hernan Amartino ◽  
Marina Szlago
Keyword(s):  
Enzyme Replacement Therapy ◽  
Fabry Disease ◽  
Replacement Therapy ◽  
Agalsidase Beta ◽  
Enzyme Replacement
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