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Burden of disease suffered by patients with Morquio syndrome type A: results from a patient-reported outcomes survey
Molecular Genetics and Metabolism
◽
10.1016/j.ymgme.2013.12.114
◽
2014
◽
Vol 111
(2)
◽
pp. S53-S54
Author(s):
Christian J. Hendriksz
◽
Christine Lavery
◽
Christina Lampe
◽
Lisa Bell
◽
Mohit Jain
Keyword(s):
Burden Of Disease
◽
Patient Reported Outcomes
◽
Type A
◽
Syndrome Type
◽
Patient Reported
◽
Morquio Syndrome
Download Full-text
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Impact of two-year elosulfase alfa treatment on patient-reported outcomes in patients with Morquio syndrome type A: Results from an English managed access agreement
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Impact of elosulfase alfa treatment on patient-reported outcomes in Morquio syndrome type A: Results from the first year of a managed access agreement in England
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◽
First Year
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◽
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◽
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◽
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Burden of disease suffered by caregivers of patients with Morquio syndrome type A: results from a self-reported outcomes survey
Molecular Genetics and Metabolism
◽
10.1016/j.ymgme.2013.12.146
◽
2014
◽
Vol 111
(2)
◽
pp. S65
Author(s):
Christina Lampe
◽
Christian J. Hendriksz
◽
Christine Lavery
◽
Lisa Bell
◽
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Keyword(s):
Burden Of Disease
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Type A
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Faculty Opinions recommendation of Botulinum toxin type A treatment of multiple upper facial sites: patient-reported outcomes.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.1066975.519943
◽
2007
◽
Author(s):
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Keyword(s):
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The patient experience of elosulfase alfa treatment for MPS IVA (Morquio syndrome type A): beyond traditional measures
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◽
Mps Iva
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Patient-reported outcomes in subjects receiving botulinum toxin type A (BoNTA) treatment for moderate to severe glabellar rhytids: Results from two randomized, double-blind, placebo-controlled studies
Journal of the American Academy of Dermatology
◽
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◽
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◽
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◽
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Keyword(s):
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Type A
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◽
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Psychological health in adults with Morquio syndrome type A after six months of enzyme replacement therapy
Molecular Genetics and Metabolism
◽
10.1016/j.ymgme.2019.11.021
◽
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◽
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◽
pp. S19-S20
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◽
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◽
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◽
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Airway stenting in MPS IVA (Morquio syndrome type A)
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Analysis of C6S/C4S ratio in Morquio syndrome type A patients
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Elosulfase alfa treatment and changes in physical functioning and disability in Morquio syndrome type A
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