scholarly journals 142. Serotype Optimization of an AAV Vector for Gene Therapy in Canine and Murine Glycogen Storage Disease Type Ia (GSD-Ia)

2010 ◽  
Vol 18 ◽  
pp. S54-S55
Keyword(s):  
Gene Therapy ◽  
Glycogen Storage Disease ◽  
Storage Disease ◽  
Glycogen Storage Disease Type ◽  
Glycogen Storage ◽  
Disease Type ◽  
Aav Vector ◽  
Type Ia

scholarly journals Bezafibrate Enhances AAV Vector-Mediated Genome Editing in Glycogen Storage Disease Type Ia

2019 ◽  
Vol 13 ◽  
pp. 265-273 ◽  
Author(s):  
Hye-Ri Kang ◽  
Lauren Waskowicz ◽  
Andrea M. Seifts ◽  
Dustin J. Landau ◽  
Sarah P. Young ◽  
...  
Keyword(s):  
Genome Editing ◽  
Glycogen Storage Disease ◽  
Storage Disease ◽  
Glycogen Storage Disease Type ◽  
Glycogen Storage ◽  
Disease Type ◽  
Aav Vector ◽  
Type Ia

scholarly journals Downregulation of pathways implicated in liver inflammation and tumorigenesis of glycogen storage disease type Ia mice receiving gene therapy

2017 ◽  
Vol 26 (10) ◽  
pp. 1890-1899 ◽  
Author(s):  
Goo-Young Kim ◽  
Joon Hyun Kwon ◽  
Jun-Ho Cho ◽  
Lisa Zhang ◽  
Brian C. Mansfield ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Glycogen Storage Disease ◽  
Storage Disease ◽  
Glycogen Storage Disease Type ◽  
Glycogen Storage ◽  
Disease Type ◽  
Liver Inflammation ◽  
Type Ia

scholarly journals AAV Vector-mediated Reversal of Hypoglycemia in Canine and Murine Glycogen Storage Disease Type Ia

2008 ◽  
Vol 16 (4) ◽  
pp. 665-672 ◽  
Author(s):  
Dwight D Koeberl ◽  
Carlos Pinto ◽  
Baodong Sun ◽  
Songtao Li ◽  
Daniel M Kozink ◽  
...  
Keyword(s):  
Glycogen Storage Disease ◽  
Storage Disease ◽  
Glycogen Storage Disease Type ◽  
Glycogen Storage ◽  
Disease Type ◽  
Aav Vector ◽  
Type Ia

scholarly journals Corrigendum to “Efficacy of Helper-dependent Adenovirus Vector-mediated Gene Therapy in Murine Glycogen Storage Disease Type Ia”

2007 ◽  
Vol 15 (11) ◽  
pp. 2051
Author(s):  
Dwight D Koeberl ◽  
Baodong Sun ◽  
Andrew Bird ◽  
Yuan-Tsong Chen ◽  
Kazuhiro Oka ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Glycogen Storage Disease ◽  
Storage Disease ◽  
Adenovirus Vector ◽  
Glycogen Storage Disease Type ◽  
Glycogen Storage ◽  
Disease Type ◽  
Type Ia

scholarly journals Complete Normalization of Hepatic G6PC Deficiency in Murine Glycogen Storage Disease Type Ia Using Gene Therapy

2010 ◽  
Vol 18 (6) ◽  
pp. 1076-1084 ◽  
Author(s):  
Wai Han Yiu ◽  
Young Mok Lee ◽  
Wen-Tao Peng ◽  
Chi-Jiunn Pan ◽  
Paul A Mead ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Glycogen Storage Disease ◽  
Storage Disease ◽  
Glycogen Storage Disease Type ◽  
Glycogen Storage ◽  
Disease Type ◽  
Type Ia
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