Onasemnogene Abeparvovec Gene-Replacement Therapy (GRT) for Spinal Muscular Atrophy Type 1 (SMA1): Pivotal Phase 3 Study (STR1VE) Update

2019 ◽  
Author(s):  
John W. Day ◽  
Claudia A. Chiriboga ◽  
Thomas O. Crawford ◽  
Basil T. Darras ◽  
Richard S. Finkel ◽  
...  
2018 ◽  
Vol 54 (2) ◽  
pp. 179-185 ◽  
Author(s):  
Samiah Al‐Zaidy ◽  
A. Simon Pickard ◽  
Kavitha Kotha ◽  
Lindsay N. Alfano ◽  
Linda Lowes ◽  
...  

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