Gene Therapy Clinical Trials for Adenosine Deaminase Deficiency/Severe Combined Immunodeficiency

Clinical Trials of Genetic Therapy with Antisense DNA and DNA Vectors ◽

10.1201/9781003064657-6 ◽

2020 ◽

pp. 111-131

Author(s):

Eriinda M. Gordon ◽

W. French Anderson

Keyword(s):

Gene Therapy ◽

Clinical Trials ◽

Adenosine Deaminase ◽

Severe Combined Immunodeficiency ◽

Combined Immunodeficiency ◽

Adenosine Deaminase Deficiency

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Gene Therapy Clinical Trials for Adenosine Deaminase Deficiency/Severe Combined Immunodeficiency

Clinical Trials of Genetic Therapy with Antisense DNA and DNA Vectors ◽

10.4324/9781003064657-6 ◽

2020 ◽

pp. 111-131

Author(s):

Eriinda M. Gordon ◽

W. French Anderson

Keyword(s):

Gene Therapy ◽

Clinical Trials ◽

Adenosine Deaminase ◽

Severe Combined Immunodeficiency ◽

Combined Immunodeficiency ◽

Adenosine Deaminase Deficiency

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Gene Therapy for Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency: Improved Retroviral Vectors for Clinical Trials

Acta Haematologica ◽

10.1159/000040930 ◽

1999 ◽

Vol 101 (2) ◽

pp. 89-96 ◽

Author(s):

Masafumi Onodera ◽

DavidM. Nelson ◽

Yukio Sakiyama ◽

Fabio Candotti ◽

R.Michael Blaese

Keyword(s):

Gene Therapy ◽

Clinical Trials ◽

Adenosine Deaminase ◽

Severe Combined Immunodeficiency ◽

Retroviral Vectors ◽

Combined Immunodeficiency ◽

Adenosine Deaminase Deficiency

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Severe combined immunodeficiency disease, adenosine deaminase deficiency and gene therapy

Current Opinion in Immunology ◽

10.1016/0952-7915(91)90019-w ◽

1991 ◽

Vol 3 (4) ◽

pp. 547-551 ◽

Author(s):

Robertson Parkman ◽

Erwin W Gelfand

Keyword(s):

Gene Therapy ◽

Adenosine Deaminase ◽

Severe Combined Immunodeficiency ◽

Combined Immunodeficiency ◽

Adenosine Deaminase Deficiency ◽

Immunodeficiency Disease ◽

Severe Combined Immunodeficiency Disease

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Gene Therapy for Severe Combined Immunodeficiency due to Adenosine Deaminase Deficiency

Current Gene Therapy ◽

10.2174/156652312799789253 ◽

2012 ◽

Vol 12 (1) ◽

pp. 57-65 ◽

Author(s):

Claudia A. Montiel-Equihua ◽

Adrian J. Thrasher ◽

H. Bobby Gaspar

Keyword(s):

Gene Therapy ◽

Adenosine Deaminase ◽

Severe Combined Immunodeficiency ◽

Combined Immunodeficiency ◽

Adenosine Deaminase Deficiency

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Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis

10.1002/hep.30160 ◽

2018 ◽

Vol 68 (6) ◽

pp. 2434-2437 ◽

Author(s):

Francesca Tucci ◽

Valeria Calbi ◽

Federica Barzaghi ◽

Maddalena Migliavacca ◽

Francesca Ferrua ◽

...

Keyword(s):

Gene Therapy ◽

Adenosine Deaminase ◽

Successful Treatment ◽

Severe Combined Immunodeficiency ◽

Combined Immunodeficiency ◽

Adenosine Deaminase Deficiency

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Development of gene therapy: potential in severe combined immunodeficiency due to adenosine deaminase deficiency

Stem Cells and Cloning Advances and Applications ◽

10.2147/sccaa.s5570 ◽

2009 ◽

pp. 1

Author(s):

Adrian Thrasher ◽

Montiel-Equihua ◽

Bobby Gaspar

Keyword(s):

Gene Therapy ◽

Adenosine Deaminase ◽

Severe Combined Immunodeficiency ◽

Combined Immunodeficiency ◽

Adenosine Deaminase Deficiency

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Identification and quantitation of adenine deoxynucleotides in erythrocytes of a patient with adenosine deaminase deficiency and severe combined immunodeficiency.

Journal of Biological Chemistry ◽

10.1016/s0021-9258(17)34910-4 ◽

1978 ◽

Vol 253 (5) ◽

pp. 1619-1626

Author(s):

M.S. Coleman ◽

J. Donofrio ◽

J.J. Hutton ◽

L. Hahn ◽

A. Daoud ◽

...

Keyword(s):

Adenosine Deaminase ◽

Severe Combined Immunodeficiency ◽

Combined Immunodeficiency ◽

Adenosine Deaminase Deficiency

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Multicentric dermatofibrosarcoma protuberans in a child with severe combined immunodeficiency due to adenosine deaminase deficiency

Pediatric Dermatology ◽

10.1111/pde.14597 ◽

2021 ◽

Author(s):

Tatjana D. Wahjudi ◽

Heinz Kutzner ◽

Matthias Bleeke ◽

Peter H. Hoeger

Keyword(s):

Adenosine Deaminase ◽

Severe Combined Immunodeficiency ◽

Dermatofibrosarcoma Protuberans ◽

Combined Immunodeficiency ◽

Adenosine Deaminase Deficiency

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Adenosine Deaminase Deficiency and Severe Combined Immunodeficiency Disease

Advances in Enzymology - and Related Areas of Molecular Biology - Advances in Enzymology and Related Areas of Molecular Biology ◽

10.1002/9780470122969.ch4 ◽

2006 ◽

pp. 167-210 ◽

Author(s):

Linda F. Thompson ◽

J. Edwin Seegmiller

Keyword(s):

Adenosine Deaminase ◽

Severe Combined Immunodeficiency ◽

Combined Immunodeficiency ◽

Adenosine Deaminase Deficiency ◽

Immunodeficiency Disease ◽

Severe Combined Immunodeficiency Disease

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Adenosine deaminase activity in normal tissues and tissues from a child with severe combined immunodeficiency and adenosine deaminase deficiency

Clinical Immunology and Immunopathology ◽

10.1016/0090-1229(78)90100-9 ◽

1978 ◽

Vol 9 (3) ◽

pp. 287-292 ◽

Author(s):

Rochelle Hirschhorn ◽

Frank Martiniuk ◽

Fred S. Rosen

Keyword(s):

Adenosine Deaminase ◽

Severe Combined Immunodeficiency ◽

Combined Immunodeficiency ◽

Adenosine Deaminase Deficiency ◽

Normal Tissues ◽

Adenosine Deaminase Activity

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