Next-generation antibody-guided enzyme replacement therapy for lysosomal storage diseases

Replacement Therapy ◽

Next Generation ◽

Lysosomal Storage ◽

Storage Diseases ◽

Management of hypersensitivity reactions to enzyme replacement therapy in children with lysosomal storage diseases

Annals of Allergy Asthma & Immunology ◽

10.1016/j.anai.2020.07.010 ◽

2020 ◽

Vol 125 (4) ◽

pp. 460-467

Author(s):

Irem Turgay Yagmur ◽

Ozlem Unal Uzun ◽

Aynur Kucukcongar Yavas ◽

Ilknur Kulhas Celik ◽

Muge Toyran ◽

...

Keyword(s):

Replacement Therapy ◽

Hypersensitivity Reactions ◽

Lysosomal Storage ◽

Storage Diseases ◽

Promising CNS-directed enzyme replacement therapy for lysosomal storage diseases

Experimental Neurology ◽

10.1016/j.expneurol.2009.03.040 ◽

2009 ◽

Vol 218 (1) ◽

pp. 5-8 ◽

Cited By ~ 12

Author(s):

Shannon L. Macauley ◽

Mark S. Sands

Keyword(s):

Replacement Therapy ◽

Lysosomal Storage ◽

Storage Diseases ◽

Musings on genome medicine: enzyme-replacement therapy of the lysosomal storage diseases

Genome Medicine ◽

10.1186/gm114 ◽

2009 ◽

Vol 1 (12) ◽

pp. 114 ◽

Cited By ~ 3

Author(s):

David G Nathan ◽

Stuart H Orkin

Keyword(s):

Replacement Therapy ◽

Lysosomal Storage ◽

Storage Diseases ◽

Enzyme Replacement ◽

Genome Medicine

New Strategies for Enzyme Replacement Therapy for Lysosomal Storage Diseases

Rejuvenation Research ◽

10.1089/rej.2009.0920 ◽

2010 ◽

Vol 13 (2-3) ◽

pp. 229-236 ◽

Cited By ~ 51

Author(s):

Jeffrey H. Grubb ◽

Carole Vogler ◽

William S. Sly

Keyword(s):

Replacement Therapy ◽

Lysosomal Storage ◽

Storage Diseases ◽

Enzyme Replacement ◽

New Strategies

Intracisternal enzyme replacement therapy in lysosomal storage diseases: dispersal pathways, regional enzyme concentrations and the effect of posttreatment posture

Neuropathology and Applied Neurobiology ◽

10.1111/nan.12010 ◽

2013 ◽

Vol 39 (6) ◽

pp. 681-692 ◽

Cited By ~ 8

Author(s):

R. D. Jolly ◽

N. R. Marshall ◽

J. Marshall ◽

A. Hartman ◽

K. M. Hemsley ◽

...

Keyword(s):

Replacement Therapy ◽

Lysosomal Storage ◽

Storage Diseases ◽

Enzyme Replacement Therapy in Lysosomal Storage Diseases

Rare Diseases - Advances in Predictive, Preventive and Personalised Medicine ◽

10.1007/978-94-017-9214-1_7 ◽

2014 ◽

pp. 91-107

Author(s):

Vassili Valayannopoulos

Keyword(s):

Replacement Therapy ◽

Lysosomal Storage ◽

Storage Diseases ◽

P26—Anti-CD3 Antibody Reduces AntibodY Formation and Prevents Potentially Fatal Hypersensitivity Reaction in Enzyme-Replacement Therapy for Murine Lysosomal Storage Diseases

Clinical Therapeutics ◽

10.1016/j.clinthera.2012.03.055 ◽

2012 ◽

Vol 34 (4) ◽

pp. e28

Author(s):

T. Ohashi

Keyword(s):

Hypersensitivity Reaction ◽

Replacement Therapy ◽

Antibody Formation ◽

Lysosomal Storage ◽

Storage Diseases ◽

Enzyme replacement therapy for lysosomal storage diseases

Current Opinion in Pediatrics ◽

10.1097/mop.0b013e32834c20d9 ◽

2011 ◽

Vol 23 (6) ◽

pp. 588-593 ◽

Cited By ~ 66

Author(s):

Robin H. Lachmann

Keyword(s):

Replacement Therapy ◽

Lysosomal Storage ◽

Storage Diseases ◽

Current Enzyme Replacement Therapy for the Treatment of Lysosomal Storage Diseases

Pediatric Annals ◽

10.3928/00904481-20090723-09 ◽

2009 ◽

Vol 38 (8) ◽

pp. 448-455 ◽

Cited By ~ 23

Author(s):

Elizabeth R. Lim-Melia ◽

David F. Kronn

Keyword(s):

Replacement Therapy ◽

Lysosomal Storage ◽

Storage Diseases ◽

Maximizing the therapeutic potential of enzyme replacement therapy for lysosomal storage diseases

International Journal of Clinical Pharmacology and Therapeutics ◽

10.5414/cpp47707 ◽

2009 ◽

Vol 47 (12) ◽

pp. 707-708 ◽

Cited By ~ 1

Author(s):

V. Gieselmann

Keyword(s):

Replacement Therapy ◽

Therapeutic Potential ◽

Lysosomal Storage ◽

Storage Diseases ◽