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Orphan designation: Sodium benzoate, Treatment of argininosuccinic aciduria
Case Medical Research
◽
10.31525/cmr-1a95680
◽
2019
◽
Author(s):
Keyword(s):
Sodium Benzoate
◽
Orphan Designation
◽
Argininosuccinic Aciduria
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Orphan designation: Sodium benzoate,Sodium phenylacetate, Treatment of argininosuccinic aciduria
Case Medical Research
◽
10.31525/cmr-1f3d2f9
◽
2019
◽
Author(s):
Keyword(s):
Sodium Benzoate
◽
Orphan Designation
◽
Argininosuccinic Aciduria
◽
Sodium Phenylacetate
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Orphan designation: Glyceryl tri-(4-phenylbutyrate), Treatment of argininosuccinic aciduria
Case Medical Research
◽
10.31525/cmr-1780039
◽
2019
◽
Author(s):
Keyword(s):
Orphan Designation
◽
Argininosuccinic Aciduria
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Orphan designation: Sodium benzoate, Treatment of hyperargininaemia
Case Medical Research
◽
10.31525/cmr-1a95684
◽
2019
◽
Author(s):
Keyword(s):
Sodium Benzoate
◽
Orphan Designation
Download Full-text
Orphan designation: Sodium benzoate,Sodium phenylacetate, Treatment of ornithine transcarbamylase deficiency
Case Medical Research
◽
10.31525/cmr-152a1a0
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2019
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Author(s):
Keyword(s):
Sodium Benzoate
◽
Ornithine Transcarbamylase
◽
Ornithine Transcarbamylase Deficiency
◽
Orphan Designation
◽
Sodium Phenylacetate
Download Full-text
Orphan designation: Sodium benzoate, sodium phenylacetate, Treatment of citrullinaemia type 1
Case Medical Research
◽
10.31525/cmr-1a07d45
◽
2019
◽
Author(s):
Keyword(s):
Sodium Benzoate
◽
Orphan Designation
◽
Sodium Phenylacetate
Download Full-text
Orphan designation: Sodium benzoate,Sodium phenylacetate, Treatment of hyperargininaemia
Case Medical Research
◽
10.31525/cmr-1f3d2f6
◽
2019
◽
Author(s):
Keyword(s):
Sodium Benzoate
◽
Orphan Designation
◽
Sodium Phenylacetate
Download Full-text
Orphan designation: Sodium benzoate, sodium phenylacetate, Treatment of carbamoyl-phosphate synthase-1 deficiency
Case Medical Research
◽
10.31525/cmr-1a07d3d
◽
2019
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Author(s):
Keyword(s):
Sodium Benzoate
◽
Carbamoyl Phosphate
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Orphan Designation
◽
Sodium Phenylacetate
◽
Phosphate Synthase
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Strength features of humerus in rats with defects in tibiae after 60-day administration of sodium benzoate
Bone Abstracts
◽
10.1530/boneabs.3.pp35
◽
2014
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Author(s):
Galina Lukyantseva
◽
Vladyslav Luzin
Keyword(s):
Sodium Benzoate
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Orphan designation: Anti-neonatal Fc receptor human monoclonal antibody, Prevention of haemolytic disease of the foetus and newborn
Case Medical Research
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10.31525/cmr-277ad45
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2020
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Author(s):
Keyword(s):
Monoclonal Antibody
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Human Monoclonal Antibody
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Fc Receptor
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Neonatal Fc Receptor
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Haemolytic Disease
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Orphan Designation
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Orphan designation: (4R,5R)-1-[[4-[[4-[3,3-dibutyl-7-(dimethylamino)-2,3,4,5- tetrahydro-4-hydroxy-1,1-dioxido-1-benzothiepin-5-yl]phenoxy]methyl]phenyl]methyl]-4-aza-1-azoniabicyclo[2.2.2]octane chloride, Treatment of primary biliary cirrhosis
Case Medical Research
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10.31525/cmr-277ad3d
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2020
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Author(s):
Keyword(s):
Primary Biliary Cirrhosis
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Biliary Cirrhosis
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Orphan Designation
◽
Chloride Treatment
◽
Methyl Phenyl
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