Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database
2017 ◽
Vol 4
(4)
◽
pp. 293-306
◽
Zaïda Koeks
◽
Catherine L. Bladen
◽
David Salgado
◽
Erik van Zwet
◽
Oksana Pogoryelova
◽
...
2015 ◽
Vol 25
◽
pp. S302-S303
N. Alshaikh
◽
A. Brunklaus
◽
S. Robb
◽
R. Quinlivan
◽
P. Munot
◽
...
2015 ◽
Vol 36
(4)
◽
pp. 395-402
◽
Catherine L. Bladen
◽
David Salgado
◽
Soledad Monges
◽
Maria E. Foncuberta
◽
Kyriaki Kekou
◽
...
2019 ◽
Vol 3
(Supplement_1)
◽
Claire Wood
◽
Volker Straub
◽
Michela Guglieri
◽
Tim Cheetham
2017 ◽
Vol 27
(8)
◽
pp. 730-737
◽
Sunkyung Kim
◽
Yong Zhu
◽
Paul A. Romitti
◽
Deborah J. Fox
◽
Daniel W. Sheehan
◽
...
C. L. Wood
◽
T. D Cheetham
◽
K. G Hollingsworth
◽
M. Guglieri
◽
Y. Ailins-Sahun
◽
...
2017 ◽
Vol 21
◽
pp. e235-e236
H.J.A. van Ruiten
◽
A.C. Jimenez-Moreno
◽
E. Elliot
◽
A. Mayhew
◽
M. James
◽
...
C. McDonald
◽
H. Gordish-Dressman
◽
M. Leinonen
◽
O. Mayer
2011 ◽
Vol 2011
◽
pp. 198-199