Gene Therapy for Huntington’s Disease Using Targeted Endonucleases

2019 ◽  
pp. 269-284 ◽  
Author(s):  
Magdalena Dabrowska ◽  
Marta Olejniczak
Keyword(s):  
Gene Therapy ◽  
Huntington's Disease ◽  
Huntington’S Disease

L5 Pre-clinical evaluation of aav5-mihtt gene therapy of huntington’s disease in rodents

2016 ◽  
Vol 87 (Suppl 1) ◽  
pp. A91.3-A92
Author(s):  
Jana Miniarikova ◽  
Ilaria Zanella ◽  
Bas Blits ◽  
Melvin Evers ◽  
Virginie Zimmer ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Huntington's Disease ◽  
Huntington’S Disease ◽  
Clinical Evaluation

scholarly journals Combination of stem cell and gene therapy ameliorates symptoms in Huntington’s disease mice

2019 ◽  
Vol 4 (1) ◽  
Author(s):  
In Ki Cho ◽  
Carissa Emerson Hunter ◽  
Sarah Ye ◽  
Alvince Learnz Pongos ◽  
Anthony Wing Sang Chan
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Huntington's Disease ◽  
Huntington’S Disease ◽  
Cell And Gene Therapy

Gene therapy for Huntington's disease

2012 ◽  
Vol 48 (2) ◽  
pp. 243-254 ◽  
Author(s):  
Shilpa Ramaswamy ◽  
Jeffrey H. Kordower
Keyword(s):  
Gene Therapy ◽  
Huntington's Disease ◽  
Huntington’S Disease

M01 Rnai-based Gene Therapy Of Huntington's Disease

2014 ◽  
Vol 85 (Suppl 1) ◽  
pp. A94-A94
Author(s):  
P. Konstantinova ◽  
J. Miniarikova ◽  
E. Hanenmaaijer ◽  
R. Martier ◽  
B. Blits ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Huntington's Disease ◽  
Huntington’S Disease

scholarly journals AAV1/2-mediated BDNF gene therapy in a transgenic rat model of Huntington’s disease

Gene Therapy ◽  
2015 ◽  
Vol 23 (3) ◽  
pp. 283-295 ◽  
Author(s):  
B Connor ◽  
Y Sun ◽  
D von Hieber ◽  
S K Tang ◽  
K S Jones ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Huntington's Disease ◽  
Huntington’S Disease ◽  
Rat Model ◽  
Transgenic Rat ◽  
Bdnf Gene ◽  
Transgenic Rat Model

scholarly journals AAV5-miHTT gene therapy demonstrates suppression of mutant huntingtin aggregation and neuronal dysfunction in a rat model of Huntington’s disease

Gene Therapy ◽  
2017 ◽  
Vol 24 (10) ◽  
pp. 630-639 ◽  
Author(s):  
J Miniarikova ◽  
V Zimmer ◽  
R Martier ◽  
C C Brouwers ◽  
C Pythoud ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Huntington's Disease ◽  
Huntington’S Disease ◽  
Rat Model ◽  
Neuronal Dysfunction ◽  
Mutant Huntingtin
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