Early administration of enzyme replacement therapy for Pompe disease: Short-term follow-up results

2008 ◽  
Vol 31 (S2) ◽  
pp. 431-436 ◽  
Author(s):  
M. A. Hamdan ◽  
M. H. Almalik ◽  
H. M. Mirghani
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Pompe Disease ◽  
Short Term ◽  
Early Administration ◽  
Enzyme Replacement

scholarly journals Quality of life and participation in daily life of adults with Pompe disease receiving enzyme replacement therapy: 10 years of international follow-up

2015 ◽  
Vol 39 (2) ◽  
pp. 253-260 ◽  
Author(s):  
Deniz Güngör ◽  
Michelle E. Kruijshaar ◽  
Iris Plug ◽  
Dimitris Rizopoulos ◽  
Tim A. Kanters ◽  
...  
Keyword(s):  
Quality Of Life ◽  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Pompe Disease ◽  
Daily Life ◽  
Enzyme Replacement

Muscular Strength and Function in Late-Onset Pompe Disease: Five-Year Follow-Up of Patients Receiving Enzyme Replacement Therapy

2011 ◽  
Vol 33 (6) ◽  
pp. S37
Author(s):  
Paula Garcia ◽  
Rui Castelo ◽  
Mafalda Barbosa ◽  
Henriqueta Araujo ◽  
Vera Ribeiro ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Pompe Disease ◽  
Muscular Strength ◽  
Late Onset ◽  
Enzyme Replacement ◽  
And Function

scholarly journals Long-term follow-up of 17 patients with childhood Pompe disease treated with enzyme replacement therapy

2018 ◽  
Vol 41 (6) ◽  
pp. 1205-1214 ◽  
Author(s):  
Jan C. van der Meijden ◽  
Michelle E. Kruijshaar ◽  
Laurike Harlaar ◽  
Dimitris Rizopoulos ◽  
Nadine A. M. E. van der Beek ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Pompe Disease ◽  
Enzyme Replacement ◽  
Long Term Follow Up

36-Months follow-up assessment after cessation and resuming of enzyme replacement therapy in late onset Pompe disease: data from the Swiss Pompe Registry

2018 ◽  
Vol 265 (12) ◽  
pp. 2783-2788 ◽  
Author(s):  
Olivier Scheidegger ◽  
Daniela Leupold ◽  
Rafael Sauter ◽  
Oliver Findling ◽  
Kai Michael Rösler ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Pompe Disease ◽  
Late Onset ◽  
Enzyme Replacement

Effect of enzyme replacement therapy in late onset Pompe disease: open pilot study of 48 weeks follow-up

2014 ◽  
Vol 36 (4) ◽  
pp. 599-605 ◽  
Author(s):  
Jin-Sung Park ◽  
Hye-Gyung Kim ◽  
Jin-Hong Shin ◽  
Young-Chul Choi ◽  
Dae-Seong Kim
Keyword(s):  
Pilot Study ◽  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Pompe Disease ◽  
Late Onset ◽  
Enzyme Replacement ◽  
Open Pilot
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