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Cytotherapy ◽  
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Jennifer Wherley ◽  
Sabine Geiger ◽  
Beatriz Campo Fernandez ◽  
Michael L. Kaufman ◽  
...  
Keyword(s):  
Clinical Trial ◽  
Gene Therapy ◽  
Phase 1 ◽  
Preclinical Studies ◽  
Cell Disease ◽  
Hematopoietic Stem ◽  
Phase 1 Clinical Trial ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

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Author(s):  
Niek P. van Til ◽  
Yildirim Dogan ◽  
Cecilia Barese ◽  
Zeenath Unnisa ◽  
Swaroopa Guda ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Hematopoietic Stem Cell ◽  
Preclinical Study ◽  
Hematopoietic Stem ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

scholarly journals Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE

2018 ◽  
Vol 8 ◽  
pp. 152-165 ◽  
Author(s):  
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Raquel Cabrera-Pérez ◽  
Javier Torres-Torronteras ◽  
Marianna Bugiani ◽  
Joost C. Haeck ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Mouse Model ◽  
Safety Evaluation ◽  
Efficacy And Safety ◽  
Hematopoietic Stem ◽  
Preclinical Efficacy ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy
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