PRO10 USE OF SINGLE DOSE GENE-REPLACEMENT THERAPY FOR THE TREATMENT OF SPINAL MUSCULAR ATROPHY TYPE 1: A UNITED STATES PAYER BUDGET IMPACT ANALYSIS
2019 ◽
Vol 22
◽
pp. S336-S337
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D. Malone
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B. Miller
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R. Dean
◽
R. Arjunji
◽
I.S. Jensen
◽
...
2019 ◽
Vol 22
◽
pp. S42-S43
◽
D. Malone
◽
R. Dean
◽
B. Miller
◽
R. Arjunji
◽
D.E. Feltner
◽
...
R. Dean
◽
B. Miller
◽
R. Arjunji
◽
H. Awano
◽
A. Igarashi
◽
...
Francesco Muntoni
◽
Giovanni Baranello
◽
Claudio Bruno
◽
Stefania Corti
◽
Riccardo Masson
◽
...
J. Day
◽
C. Chiriboga
◽
T. Crawford
◽
B. Darras
◽
R. Finkel
◽
...
O. Dabbous
◽
D.M. Sproule
◽
D.E. Feltner
◽
M. Droege
◽
F. Khan
◽
...
J.R. Mendell
◽
S. Al-Zaidy
◽
R. Shell
◽
W.D. Arnold
◽
L. Rodino-Klapac
◽
...
John W. Day
◽
Claudia A. Chiriboga
◽
Thomas O. Crawford
◽
Basil T. Darras
◽
Richard S. Finkel
◽
...
R. Shell
◽
J.W. Day
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C. Chiriboga
◽
T.O. Crawford
◽
B.T. Darras
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...
2018 ◽
Vol 54
(2)
◽
pp. 179-185
◽
Samiah Al‐Zaidy
◽
A. Simon Pickard
◽
Kavitha Kotha
◽
Lindsay N. Alfano
◽
Linda Lowes
◽
...