Design of a phase 3 trial to evaluate the long-term efficacy and safety of ataluren in patients with nonsense mutation Duchenne muscular dystrophy

2017 ◽  
Vol 27 ◽  
pp. S218
Author(s):  
P. Riebling ◽  
E. O'Mara ◽  
X. Luo ◽  
P. Trifillis ◽  
T. Ong
Keyword(s):  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy ◽  
Nonsense Mutation ◽  
Efficacy And Safety ◽  
Phase 3 ◽  
Term Efficacy

Long-term Efficacy and Safety of Brodalumab in Patients With Psoriasis Disease Duration <10 and ≥10 Years: Analysis of Two Phase 3 Studies

2019 ◽  
Vol 3 ◽  
pp. S25
Author(s):  
Benjamin Ehst ◽  
George Han ◽  
Scott Guenthner ◽  
Kimberly Eads ◽  
Abby Jacobson
Keyword(s):  
Disease Duration ◽  
Efficacy And Safety ◽  
Phase 3 ◽  
Two Phase ◽  
Term Efficacy

Abstract not available.

scholarly journals Long-Term Efficacy and Safety of Hizentra® in Patients with Primary Immunodeficiency in Japan, Europe, and the United States: a Review of 7 Phase 3 Trials

2018 ◽  
Vol 38 (8) ◽  
pp. 864-875 ◽  
Author(s):  
Stephen Jolles ◽  
Mikhail A. Rojavin ◽  
John-Philip Lawo ◽  
Robert Nelson ◽  
Richard L. Wasserman ◽  
...  
Keyword(s):  
United States ◽  
Primary Immunodeficiency ◽  
The United States ◽  
Efficacy And Safety ◽  
Phase 3 ◽  
Term Efficacy

Lung Function in Ataluren-Treated, Nonambulatory Patients with Nonsense Mutation Duchenne Muscular Dystrophy from a Long-Term Extension Trial

2017 ◽  
Vol 48 (S 01) ◽  
pp. S1-S45 ◽  
Author(s):  
C. Werner ◽  
H. Kroger ◽  
X. Luo ◽  
J. McIntosh ◽  
P. Trifillis ◽  
...  
Keyword(s):  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy ◽  
Lung Function ◽  
Nonsense Mutation ◽  
Extension Trial

scholarly journals Long-term efficacy and safety of secukinumab in patients with psoriatic arthritis: 5-year (end-of-study) results from the phase 3 FUTURE 2 study

2020 ◽  
Vol 2 (4) ◽  
pp. e227-e235 ◽  
Author(s):  
Iain B McInnes ◽  
Philip J Mease ◽  
Alan J Kivitz ◽  
Peter Nash ◽  
Proton Rahman ◽  
...  
Keyword(s):  
Psoriatic Arthritis ◽  
Efficacy And Safety ◽  
Phase 3 ◽  
Term Efficacy ◽  
Study Results ◽  
Future 2
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