ScienceGate
Advanced Search
Author Search
Journal Finder
Blog
Sign in / Sign up
ScienceGate
Search
Author Search
Journal Finder
Blog
Sign in / Sign up
Immune function in X-linked retinoschisis subjects in an AAV8-RS1 phase I/IIa gene therapy trial
Molecular Therapy
◽
10.1016/j.ymthe.2021.02.013
◽
2021
◽
Author(s):
Alaknanda Mishra
◽
Camasamudram Vijayasarathy
◽
Catherine A. Cukras
◽
Henry E. Wiley
◽
H. Nida Sen
◽
...
Keyword(s):
Gene Therapy
◽
Phase I
◽
Immune Function
◽
Gene Therapy Trial
◽
Therapy Trial
Download Full-text
Related Documents
Cited By
References
Popping the Bubble: Promising Results From a Phase I-II Lentiviral Gene Therapy Trial for X-SCID
The Hematologist
◽
10.1182/hem.v16.4.9661
◽
2019
◽
Vol 16
(4)
◽
Author(s):
David T. Teachey
◽
Danielle E. Arnold
Keyword(s):
Gene Therapy
◽
Phase I
◽
Gene Therapy Trial
◽
Therapy Trial
◽
Lentiviral Gene Therapy
Download Full-text
Patient pre-selection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa.
10.26226/morressier.595a9c56d462b80296c9fadf
◽
2017
◽
Author(s):
Su Lwin
Keyword(s):
Gene Therapy
◽
Phase I
◽
Epidermolysis Bullosa
◽
Ex Vivo
◽
Dystrophic Epidermolysis Bullosa
◽
Gene Therapy Trial
◽
Recessive Dystrophic Epidermolysis Bullosa
◽
Therapy Trial
Download Full-text
A phase i hyperthermia- induced interleukin- 12 gene- therapy trial in a spontaneously arising feline soft tissue sarcoma model
International Journal of Radiation Oncology*Biology*Physics
◽
10.1016/j.ijrobp.2004.07.567
◽
2004
◽
Vol 60
(1)
◽
pp. S577
Author(s):
F. Siddiqui
◽
P.R. Avery
◽
S.M. LaRue
◽
M.L. Hauck
◽
M.W. Dewhirst
◽
...
Keyword(s):
Gene Therapy
◽
Soft Tissue
◽
Soft Tissue Sarcoma
◽
Phase I
◽
Interleukin 12
◽
Gene Therapy Trial
◽
Therapy Trial
Download Full-text
EBGene trial: patient preselection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa
British Journal of Dermatology
◽
10.1111/bjd.18559
◽
2019
◽
Vol 182
(3)
◽
pp. 794-797
◽
Cited By ~ 6
Author(s):
S. Gaucher
◽
S.M. Lwin
◽
M. Titeux
◽
A. Abdul‐Wahab
◽
N. Pironon
◽
...
Keyword(s):
Gene Therapy
◽
Phase I
◽
Epidermolysis Bullosa
◽
Ex Vivo
◽
Dystrophic Epidermolysis Bullosa
◽
Gene Therapy Trial
◽
Recessive Dystrophic Epidermolysis Bullosa
◽
Therapy Trial
Download Full-text
A phase i hyperthermia- induced interleukin- 12 gene- therapy trial in a spontaneously arising feline soft tissue sarcoma model
International Journal of Radiation Oncology*Biology*Physics
◽
10.1016/s0360-3016(04)01871-1
◽
2004
◽
Vol 60
◽
pp. S577-S577
Author(s):
F SIDDIQUI
◽
P AVERY
◽
S LARUE
◽
M HAUCK
◽
M DEWHIRST
◽
...
Keyword(s):
Gene Therapy
◽
Soft Tissue
◽
Soft Tissue Sarcoma
◽
Phase I
◽
Interleukin 12
◽
Gene Therapy Trial
◽
Therapy Trial
Download Full-text
Participant perspectives on a phase I/II ocular gene therapy trial (NCT02077361)
Ophthalmic Genetics
◽
10.1080/13816810.2019.1630843
◽
2019
◽
Vol 40
(3)
◽
pp. 276-281
Author(s):
Stephanie P. Brooks
◽
Shelly Benjaminy
◽
Tania Bubela
Keyword(s):
Gene Therapy
◽
Phase I
◽
Gene Therapy Trial
◽
Therapy Trial
◽
Participant Perspectives
Download Full-text
A phase I/II gene therapy trial in metastatic melanoma patients
Journal of the American College of Surgeons
◽
10.1016/j.jamcollsurg.2006.05.217
◽
2006
◽
Vol 203
(3)
◽
pp. S83
Author(s):
Michel Adamina
◽
Walter P. Weber
◽
Rachel Rosenthal
◽
Reto Schumacher
◽
Paul Zajac
◽
...
Keyword(s):
Gene Therapy
◽
Phase I
◽
Metastatic Melanoma
◽
Gene Therapy Trial
◽
Melanoma Patients
◽
Therapy Trial
Download Full-text
227 Patient pre-selection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa
Journal of Investigative Dermatology
◽
10.1016/j.jid.2017.07.224
◽
2017
◽
Vol 137
(10)
◽
pp. S231
Author(s):
S.M. Lwin
◽
S. Gaucher
◽
M. Titeux
◽
A. Abdul-Wahab
◽
N. Pironon
◽
...
Keyword(s):
Gene Therapy
◽
Phase I
◽
Epidermolysis Bullosa
◽
Ex Vivo
◽
Dystrophic Epidermolysis Bullosa
◽
Gene Therapy Trial
◽
Recessive Dystrophic Epidermolysis Bullosa
◽
Therapy Trial
Download Full-text
Phase I/II Gene Therapy Trial of Fanconi Anemia Patients with a New Orphan Drug Consisting of a Lentiviral Vector Carrying the FANCA Gene: A Coordinated International Action (EuroFancolen)
Human Gene Therapy Clinical Development
◽
10.1089/humc.2015.2522
◽
2015
◽
Vol 26
(2)
◽
pp. 81-82
◽
Cited By ~ 2
Keyword(s):
Gene Therapy
◽
Phase I
◽
Orphan Drug
◽
Fanconi Anemia
◽
Lentiviral Vector
◽
Gene Therapy Trial
◽
International Action
◽
Therapy Trial
Download Full-text
Design, Baseline Characteristics, and 2-Year Follow-up from The MPS IIIA Natural History Study Used as Control Group in Gene Therapy Trial
10.1055/s-0039-1685419
◽
2019
◽
Author(s):
B. Heron
◽
A. Chakrapani
◽
P. Drevot
◽
R. Giugliani
◽
N. Muschol
◽
...
Keyword(s):
Gene Therapy
◽
Natural History
◽
Control Group
◽
Natural History Study
◽
Gene Therapy Trial
◽
Baseline Characteristics
◽
Therapy Trial
◽
Mps Iiia
Download Full-text
Sign in / Sign up
Close
Export Citation Format
Close
Share Document
Close