364. Neurological Correction of Mucopolysaccharidosis IIIB Mice by Haematopoietic Stem Cell Gene Therapy
Stuart M. Ellison
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Rebecca Holley
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Daniel Fil
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John Mc Dermott
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Nisha Senthivel
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...
2014 ◽
Vol 22
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pp. S106
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2020 ◽
Vol 129
(2)
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pp. S90
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Jane Louise Kinsella
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Heather Church
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Wendy Ogden
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Ceri Jones
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Karen Buckland
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...
Helen Parker
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Stuart M Ellison
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Rebecca J Holley
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Claire O'Leary
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Aiyin Liao
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...
2006 ◽
Vol 1
(3)
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pp. 279-287
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Frank Alderuccio
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Christopher Siatskas
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James Chan
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Judith Field
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Kim Murphy
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...
2017 ◽
Vol 120
(1-2)
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pp. S28
Brian Bigger
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Stuart Ellison
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Daniel Fil
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Claire O'leary
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John McDermott
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...
2021 ◽
Vol 132
(2)
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pp. S21-S22
Valeria Calbi
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Francesca Fumagalli
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Fabiola De Mattia
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Elena Fratini
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Francesca Ferrua
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...
2019 ◽
Vol 54
(12)
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pp. 1995-2003
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Francesca Tucci
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Marta Frittoli
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Federica Barzaghi
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Valeria Calbi
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Maddalena Migliavacca
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...
Karen E Pollok
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Shanbao Cai
2003 ◽
Vol 3
(5)
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pp. 387-394
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T. Yokoo
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K. Sakurai
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T. Ohashi
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T. Kawamura