Neurological correction of mucopolysaccharidosis type IIIB mice by haematopoietic stem cell gene therapy

2017 ◽  
Vol 120 (1-2) ◽  
pp. S28
Author(s):  
Brian Bigger ◽  
Stuart Ellison ◽  
Daniel Fil ◽  
Claire O'leary ◽  
John McDermott ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Haematopoietic Stem Cell ◽  
Mucopolysaccharidosis Type ◽  
Type Iiib ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy ◽  
Mucopolysaccharidosis Type Iiib

Lentiviral mediated stem cell gene therapy corrects a mouse model of mucopolysaccharidosis type IIIA

2011 ◽  
Vol 102 (2) ◽  
pp. S8
Author(s):  
Brian Bigger ◽  
Alex Langford-Smith ◽  
Fiona Wilkinson ◽  
Kia Langford-Smith ◽  
Ana Sergijenko ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Mouse Model ◽  
Mucopolysaccharidosis Type ◽  
Type Iiia ◽  
Cell Gene ◽  
Mucopolysaccharidosis Type Iiia ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

scholarly journals 364. Neurological Correction of Mucopolysaccharidosis IIIB Mice by Haematopoietic Stem Cell Gene Therapy

2016 ◽  
Vol 24 ◽  
pp. S146
Author(s):  
Stuart M. Ellison ◽  
Rebecca Holley ◽  
Daniel Fil ◽  
John Mc Dermott ◽  
Nisha Senthivel ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Haematopoietic Stem Cell ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

scholarly journals Haematopoietic stem cell gene therapy with IL ‐1Ra rescues cognitive loss in mucopolysaccharidosis IIIA

2020 ◽  
Vol 12 (3) ◽  
Author(s):  
Helen Parker ◽  
Stuart M Ellison ◽  
Rebecca J Holley ◽  
Claire O'Leary ◽  
Aiyin Liao ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Haematopoietic Stem Cell ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

Hematopoietic Stem Cell Gene Therapy Corrects Neuropathic Phenotype in Murine Model of Mucopolysaccharidosis Type II

2015 ◽  
Vol 26 (6) ◽  
pp. 357-366 ◽  
Author(s):  
Taichi Wakabayashi ◽  
Yohta Shimada ◽  
Kazumasa Akiyama ◽  
Takashi Higuchi ◽  
Takahiro Fukuda ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Murine Model ◽  
Mucopolysaccharidosis Type ◽  
Type Ii ◽  
Mucopolysaccharidosis Type Ii ◽  
Hematopoietic Stem ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

Haematopoietic Stem Cell Gene Therapy to Treat Autoimmune Disease

2006 ◽  
Vol 1 (3) ◽  
pp. 279-287 ◽  
Author(s):  
Frank Alderuccio ◽  
Christopher Siatskas ◽  
James Chan ◽  
Judith Field ◽  
Kim Murphy ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Autoimmune Disease ◽  
Haematopoietic Stem Cell ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

scholarly journals Brain‐targeted stem cell gene therapy corrects mucopolysaccharidosis type II via multiple mechanisms

2018 ◽  
Vol 10 (7) ◽  
Author(s):  
Hélène FE Gleitz ◽  
Ai Yin Liao ◽  
James R Cook ◽  
Samuel F Rowlston ◽  
Gabriella MA Forte ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Mucopolysaccharidosis Type ◽  
Type Ii ◽  
Mucopolysaccharidosis Type Ii ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy
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