282. Bone Marrow Transplantation and Gene Therapy for Metachromatic Leukodystrophy

Molecular Therapy ◽

10.1016/s1525-0016(16)43112-6 ◽

2002 ◽

Vol 5 (5) ◽

pp. S94

Keyword(s):

Gene Therapy ◽

Bone Marrow ◽

Bone Marrow Transplantation ◽

Marrow Transplantation ◽

Metachromatic Leukodystrophy

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Longitudinal Neurophysiologic Studies in a Patient With Metachromatic Leukodystrophy Following Bone Marrow Transplantation

Archives of Neurology ◽

10.1001/archneur.1992.00530340114026 ◽

1992 ◽

Vol 49 (10) ◽

pp. 1088-1092 ◽

Author(s):

A. Dhuna ◽

C. Toro ◽

F. Torres ◽

W. R. Kennedy ◽

W. Krivit

Keyword(s):

Bone Marrow ◽

Bone Marrow Transplantation ◽

Marrow Transplantation ◽

Metachromatic Leukodystrophy

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Current Gene Marking and Gene Therapy Protocols for Human Bone Marrow Transplantation

Somatic Gene Therapy ◽

10.1201/9781351076760-13 ◽

2018 ◽

pp. 225-242 ◽

Author(s):

Malcolm K. Brenner

Keyword(s):

Gene Therapy ◽

Bone Marrow ◽

Bone Marrow Transplantation ◽

Marrow Transplantation ◽

Human Bone Marrow

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Bone marrow transplantation: a natural form of gene therapy

Transplantation Proceedings ◽

10.1016/s0041-1345(98)01107-5 ◽

1998 ◽

Vol 30 (7) ◽

pp. 3484-3485

Author(s):

C. Davenport ◽

S.T. Ildstad

Keyword(s):

Gene Therapy ◽

Bone Marrow ◽

Bone Marrow Transplantation ◽

Marrow Transplantation ◽

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Bone Marrow Transplantation Shows Superior Atheroprotective Effects of Gene Therapy With Apolipoprotein A-I Milano Compared With Wild-Type Apolipoprotein A-I in Hyperlipidemic Mice

Journal of the American College of Cardiology ◽

10.1016/j.jacc.2006.07.040 ◽

2006 ◽

Vol 48 (7) ◽

pp. 1459-1468 ◽

Author(s):

Lai Wang ◽

Behrooz G. Sharifi ◽

Theresa Pan ◽

Lei Song ◽

Ada Yukht ◽

...

Keyword(s):

Gene Therapy ◽

Bone Marrow ◽

Bone Marrow Transplantation ◽

Marrow Transplantation ◽

Wild Type ◽

Apolipoprotein A

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Juvenile metachromatic leukodystrophy: neurological outcome two years after bone marrow transplantation

Journal of Inherited Metabolic Disease ◽

10.1007/bf00711755 ◽

1995 ◽

Vol 18 (2) ◽

pp. 159-161 ◽

Author(s):

N. Guffon ◽

G. Souillet ◽

I. Maire ◽

C. Dorche ◽

M. Mathieu ◽

...

Keyword(s):

Bone Marrow ◽

Bone Marrow Transplantation ◽

Neurological Outcome ◽

Marrow Transplantation ◽

Metachromatic Leukodystrophy

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Bone marrow transplantation in metachromatic leukodystrophy caused by saposin-B deficiency: A case report with a 3-year follow-up period

The Journal of Pediatrics ◽

10.1016/s0022-3476(98)70191-x ◽

1998 ◽

Vol 133 (1) ◽

pp. 129-132 ◽

Author(s):

Pierre Landrieu ◽

Stéphane Blanche ◽

Marie-Thérèse Vanier ◽

Stéphane Metral ◽

B. Husson ◽

...

Keyword(s):

Bone Marrow ◽

Case Report ◽

Bone Marrow Transplantation ◽

Marrow Transplantation ◽

Metachromatic Leukodystrophy ◽

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Potential of Gene Therapy in Bone Marrow Transplantation

BioDrugs ◽

10.2165/00063030-199911010-00001 ◽

1999 ◽

Vol 11 (1) ◽

pp. 1-6

Author(s):

Sarah Marktel ◽

Chiara Bonini ◽

Claudio Bordignon

Keyword(s):

Gene Therapy ◽

Bone Marrow ◽

Bone Marrow Transplantation ◽

Marrow Transplantation

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873. Synergistic and Antagonistic Effects of Neonatal Intracranial AAV Gene Therapy and Bone Marrow Transplantation in Sanfilippo Syndrome Type B Mice

Molecular Therapy ◽

10.1016/s1525-0016(16)40276-5 ◽

2008 ◽

Vol 16 ◽

pp. S325-S326

Keyword(s):

Gene Therapy ◽

Bone Marrow ◽

Bone Marrow Transplantation ◽

Marrow Transplantation ◽

Syndrome Type ◽

Type B ◽

Sanfilippo Syndrome ◽

Antagonistic Effects ◽

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ACCELERATED RECOVERY OF IRRADIATION-INDUCED BONE MARROW DEPRESSION BY FIBROBLAST-MEDIATED INTERLEUKIN 6 GENE THERAPY IN COMBINATION WITH BONE MARROW TRANSPLANTATION IN MICE1

Transplantation Journal ◽

10.1097/00007890-199802150-00006 ◽

1998 ◽

Vol 65 (3) ◽

pp. 325-331 ◽

Author(s):

Xuetao Cao ◽

Rong Cai ◽

Dian Wen Ju ◽

Qun Tao ◽

Yizhi Yu ◽

...

Keyword(s):

Gene Therapy ◽

Bone Marrow ◽

Bone Marrow Transplantation ◽

Interleukin 6 ◽

Marrow Transplantation ◽

Bone Marrow Depression

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Bone marrow transplantation for globoid cell leukodystrophy, adrenoleukodystrophy, metachromatic leukodystrophy, and Hurler syndrome

Current Opinion in Hematology ◽

10.1097/00062752-199911000-00004 ◽

1999 ◽

Vol 6 (6) ◽

pp. 377 ◽

Author(s):

William Krivit ◽

Patrick Aubourg ◽

Elsa Shapiro ◽

Charles Peters

Keyword(s):

Bone Marrow ◽

Bone Marrow Transplantation ◽

Marrow Transplantation ◽

Metachromatic Leukodystrophy ◽

Globoid Cell Leukodystrophy ◽

Hurler Syndrome ◽

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