scholarly journals WS01.5 An open-label study of the safety, pharmacokinetics, and pharmacodynamics of ivacaftor in patients aged 2 to 5 years with cystic fibrosis and a CFTR gating mutation: The KIWI study

2015 ◽  
Vol 14 ◽  
pp. S2 ◽  
Author(s):  
M. Rosenfeld ◽  
S. Robertson ◽  
Y. Green ◽  
J. Cooke ◽  
A. Lawal ◽  
...  
2017 ◽  
Vol 16 ◽  
pp. S78 ◽  
Author(s):  
J. Taylor-Cousar ◽  
M. Jain ◽  
T.L. Barto ◽  
T. Haddad ◽  
J. Atkinson ◽  
...  

2013 ◽  
Vol 12 ◽  
pp. S15 ◽  
Author(s):  
E. Kerem ◽  
M. Wilschanski ◽  
I. Sermet-Gaudelus ◽  
K. De Boeck ◽  
F.J. Accurso ◽  
...  

2015 ◽  
Vol 14 (1) ◽  
pp. 111-119 ◽  
Author(s):  
H.A.W.M. Tiddens ◽  
K. De Boeck ◽  
J.P. Clancy ◽  
M. Fayon ◽  
Arets H.G.M. ◽  
...  

Sign in / Sign up

Export Citation Format

Share Document