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Gene Therapy with Bilirubin-UDP-Glucuronosyltransferase in the Gunn Rat Model of Crigler-Najjar Syndrome Type 1
Human Gene Therapy
◽
10.1089/hum.1998.9.4-497
◽
1998
◽
Vol 9
(4)
◽
pp. 497-505
◽
Cited By ~ 20
Author(s):
Qianhong Li
◽
Sidney S. Murphree
◽
Sharon S. Willer
◽
Roberto Bolli
◽
Brent A. French
Keyword(s):
Gene Therapy
◽
Rat Model
◽
Syndrome Type
◽
Gunn Rat
◽
Udp Glucuronosyltransferase
Download Full-text
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References
W1862 Proteoliposomes Containing Sendai Virus F-Glycoprotein for Hepatocyte-Targeted Gene Therapy of the Gunn Rat Model of Crigler-Najjar Syndrome Type 1
Gastroenterology
◽
10.1016/s0016-5085(08)63929-3
◽
2008
◽
Vol 134
(4)
◽
pp. A-840
◽
Cited By ~ 1
Author(s):
Xia Wang
◽
Debi P. Sarkar
◽
Prashant Mani
◽
Clifford J. Steer
◽
Betsy T. Kren
◽
...
Keyword(s):
Gene Therapy
◽
Rat Model
◽
Sendai Virus
◽
Syndrome Type
◽
Gunn Rat
◽
Targeted Gene Therapy
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Correction of the UDP-glucuronosyltransferase gene defect in the Gunn rat model of Crigler-Najjar syndrome type I with a chimeric oligonucleotide
Proceedings of the National Academy of Sciences
◽
10.1073/pnas.96.18.10349
◽
1999
◽
Vol 96
(18)
◽
pp. 10349-10354
◽
Cited By ~ 148
Author(s):
B. T. Kren
◽
B. Parashar
◽
P. Bandyopadhyay
◽
N. R. Chowdhury
◽
J. R. Chowdhury
◽
...
Keyword(s):
Rat Model
◽
Type I
◽
Syndrome Type
◽
Gene Defect
◽
Gunn Rat
◽
Udp Glucuronosyltransferase
Download Full-text
1037. Massive Hepatic Repopulation with Genetically Engineered Conditionally Immortalized Hepatocytes: Correction of Jaundice in the Gunn Rat Model of Crigler-Najjar Syndrome Type 1
Molecular Therapy
◽
10.1016/s1525-0016(16)43867-0
◽
2002
◽
Vol 5
(5)
◽
pp. S337
Keyword(s):
Rat Model
◽
Genetically Engineered
◽
Syndrome Type
◽
Gunn Rat
◽
Immortalized Hepatocytes
Download Full-text
88 CYCLOPHOSPHAMIDE AND NAPROXEN AUGMENT THE METABOLIC EFFECT OF HEPATOCYTE TRANSPLANTATION IN THE GUNN RAT MODEL OF CRIGLER-NAJJAR SYNDROME TYPE 1 BY ENHANCING DONOR CELL ENGRAFTMENT
Journal of Hepatology
◽
10.1016/s0168-8278(12)60102-0
◽
2012
◽
Vol 56
◽
pp. S38-S39
Author(s):
Y. Avsar
◽
H. Zhou
◽
X. Wang
◽
J. Ding
◽
C. Guha
◽
...
Keyword(s):
Rat Model
◽
Donor Cell
◽
Metabolic Effect
◽
Hepatocyte Transplantation
◽
Syndrome Type
◽
Gunn Rat
◽
Cell Engraftment
Download Full-text
535. Long-Term Correction of Hyperbilirubinemia in a Rat Model of Crigler-Najjar Syndrome Type 1
Molecular Therapy
◽
10.1016/j.ymthe.2005.07.075
◽
2005
◽
Vol 11
◽
pp. S207
Keyword(s):
Rat Model
◽
Syndrome Type
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TRPV1 Channel Contributes to the Behavioral Hypersensitivity in a Rat Model of Complex Regional Pain Syndrome Type 1
Frontiers in Pharmacology
◽
10.3389/fphar.2019.00453
◽
2019
◽
Vol 10
◽
Cited By ~ 6
Author(s):
Qimiao Hu
◽
Qiong Wang
◽
Chuan Wang
◽
Yan Tai
◽
Boyu Liu
◽
...
Keyword(s):
Complex Regional Pain Syndrome
◽
Rat Model
◽
Pain Syndrome
◽
Syndrome Type
◽
Trpv1 Channel
Download Full-text
Adenovirus-Mediated Gene Therapy to Restore Expression and Functionality of Multiple UDP-Glucuronosyltransferase 1A Enzymes in Gunn Rat Liver
Journal of Pharmacology and Experimental Therapeutics
◽
10.1124/jpet.106.104810
◽
2006
◽
Vol 318
(3)
◽
pp. 1240-1247
◽
Cited By ~ 4
Author(s):
Kristini K. Miles
◽
Fay K. Kessler
◽
Laura J. Webb
◽
Philip C. Smith
◽
Joseph K. Ritter
Keyword(s):
Gene Therapy
◽
Rat Liver
◽
Gunn Rat
◽
Udp Glucuronosyltransferase
Download Full-text
A Novel Missense Mutation of the Bilirubin UDP-Glucuronosyltransferase Gene in a Turkish Patient With Crigler-Najjar Syndrome Type 1
Journal of Pediatric Gastroenterology and Nutrition
◽
10.1097/00005176-200311000-00024
◽
2003
◽
Vol 37
(5)
◽
pp. 627-630
◽
Cited By ~ 10
Author(s):
Yoshihiro Maruo
◽
Erkin Serdaroglu
◽
Masaru Iwai
◽
Hiroko Takahashi
◽
Asami Mori
◽
...
Keyword(s):
Missense Mutation
◽
Syndrome Type
◽
Turkish Patient
◽
Udp Glucuronosyltransferase
Download Full-text
Subretinal Gene Therapy of Mice With Bardet-Biedl Syndrome Type 1
Investigative Opthalmology & Visual Science
◽
10.1167/iovs.13-11673
◽
2013
◽
Vol 54
(9)
◽
pp. 6118
◽
Cited By ~ 38
Author(s):
Seongjin Seo
◽
Robert F. Mullins
◽
Alina V. Dumitrescu
◽
Sajag Bhattarai
◽
Daniel Gratie
◽
...
Keyword(s):
Gene Therapy
◽
Syndrome Type
◽
Bardet Biedl Syndrome
Download Full-text
A Step Toward Liver Gene Therapy: Efficient Correction of the Genetic Defect of Hepatocytes Isolated From a Patient With Crigler-Najjar Syndrome Type 1 With Lentiviral Vectors
Transplantation Journal
◽
10.1097/tp.0b013e31819ca245
◽
2009
◽
Vol 87
(7)
◽
pp. 1006-1012
◽
Cited By ~ 18
Author(s):
Jacques Birraux
◽
Olivier Menzel
◽
Barbara Wildhaber
◽
Caty Jond
◽
Tuan Huy Nguyen
◽
...
Keyword(s):
Gene Therapy
◽
Genetic Defect
◽
Lentiviral Vectors
◽
Syndrome Type
◽
Liver Gene
Download Full-text
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