ScienceGate
Advanced Search
Author Search
Journal Finder
Blog
Sign in / Sign up
ScienceGate
Search
Author Search
Journal Finder
Blog
Sign in / Sign up
G140(P) Ethical considerations and challenges in long term ventilation decisions in children with spinal muscular atrophy Type –1
Archives of Disease in Childhood
◽
10.1136/archdischild-2016-310863.131
◽
2016
◽
Vol 101
(Suppl 1)
◽
pp. A74.1-A74
Author(s):
C Kanaris
Keyword(s):
Spinal Muscular Atrophy
◽
Muscular Atrophy
◽
Ethical Considerations
◽
Spinal Muscular Atrophy Type
◽
Long Term Ventilation
Download Full-text
Related Documents
Cited By
References
POINT: Is Noninvasive Ventilation Always the Most Appropriate Manner of Long-term Ventilation for Infants With Spinal Muscular Atrophy Type 1? Yes, Almost Always
CHEST Journal
◽
10.1016/j.chest.2016.11.043
◽
2017
◽
Vol 151
(5)
◽
pp. 962-965
◽
Cited By ~ 16
Author(s):
John R. Bach
Keyword(s):
Spinal Muscular Atrophy
◽
Noninvasive Ventilation
◽
Muscular Atrophy
◽
Spinal Muscular Atrophy Type
◽
Long Term Ventilation
Download Full-text
COUNTERPOINT: Is Noninvasive Ventilation Always the Most Appropriate Manner of Long-term Ventilation for Infants With Spinal Muscular Atrophy Type 1? No
CHEST Journal
◽
10.1016/j.chest.2016.11.039
◽
2017
◽
Vol 151
(5)
◽
pp. 965-968
◽
Cited By ~ 3
Author(s):
Howard B. Panitch
Keyword(s):
Spinal Muscular Atrophy
◽
Noninvasive Ventilation
◽
Muscular Atrophy
◽
Spinal Muscular Atrophy Type
◽
Long Term Ventilation
Download Full-text
Long‐term benefits of nusinersen in a child affected by cystic fibrosis and spinal muscular atrophy type 1
Pediatric Pulmonology
◽
10.1002/ppul.25334
◽
2021
◽
Author(s):
Giorgia Bruno
◽
Bernadette Donnarumma
◽
Alessia Inverardi
◽
Paolo Buonpensiero
◽
Angela Sepe
◽
...
Keyword(s):
Cystic Fibrosis
◽
Spinal Muscular Atrophy
◽
Muscular Atrophy
◽
Spinal Muscular Atrophy Type
Download Full-text
P.351Gene-replacement therapy (GRT) in spinal muscular atrophy type 1 (SMA1): long-term follow-up from the onasemnogene abeparvovec phase 1/2a clinical trial
Neuromuscular Disorders
◽
10.1016/j.nmd.2019.06.513
◽
2019
◽
Vol 29
◽
pp. S184
Author(s):
J. Mendell
◽
R. Shell
◽
K. Lehman
◽
M. McColly
◽
L. Lowes
◽
...
Keyword(s):
Clinical Trial
◽
Spinal Muscular Atrophy
◽
Replacement Therapy
◽
Muscular Atrophy
◽
Phase 1
◽
Spinal Muscular Atrophy Type
◽
Long Term Follow Up
Download Full-text
Lethal Cardiac Complications in a Long-Term Survivor of Spinal Muscular Atrophy Type 1
Kosin Medical Journal
◽
10.7180/kmj.2019.34.1.47
◽
2019
◽
Vol 34
(1)
◽
pp. 47
Author(s):
Min-Jung Cho
Keyword(s):
Spinal Muscular Atrophy
◽
Muscular Atrophy
◽
Cardiac Complications
◽
Spinal Muscular Atrophy Type
◽
Term Survivor
Download Full-text
S11 Long-term follow-up of the phase 1 START trial of onasemnogene abeparvovec gene therapy in spinal muscular atrophy type 1
10.1136/thorax-2020-btsabstracts.17
◽
2021
◽
Cited By ~ 1
Author(s):
JR Mendell
◽
R Shell
◽
KJ Lehman
◽
M McColly
◽
LP Lowes
◽
...
Keyword(s):
Gene Therapy
◽
Spinal Muscular Atrophy
◽
Muscular Atrophy
◽
Phase 1
◽
Spinal Muscular Atrophy Type
◽
Long Term Follow Up
◽
Start Trial
Download Full-text
Spinal muscular atrophy type 1: Is long-term mechanical ventilation ethical?
Journal of Paediatrics and Child Health
◽
10.1111/j.1440-1754.2007.01052.x
◽
2007
◽
Vol 43
(4)
◽
pp. 237-242
◽
Cited By ~ 20
Author(s):
Monique M Ryan
◽
Henry Kilham
◽
Stephen Jacobe
◽
Bernadette Tobin
◽
David Isaacs
Keyword(s):
Mechanical Ventilation
◽
Spinal Muscular Atrophy
◽
Muscular Atrophy
◽
Spinal Muscular Atrophy Type
Download Full-text
FV 953. Parents’ Experiences during the Compassionate Use Program (Nusinersen) for Patients with Spinal Muscular Atrophy Type 1—A Qualitative Interview Study
10.1055/s-0038-1675931
◽
2018
◽
Author(s):
Thorsten Langer
◽
Petra Kiefer
◽
Astrid Pechmann
◽
Janbernd Kirschner
Keyword(s):
Spinal Muscular Atrophy
◽
Muscular Atrophy
◽
Qualitative Interview
◽
Interview Study
◽
Compassionate Use
◽
Spinal Muscular Atrophy Type
◽
Qualitative Interview Study
◽
Parents Experiences
Download Full-text
Study Design of STR1VE-EU, a Phase 3 Trial of AVXS-101 Gene-Replacement Therapy (GRT) in Patients With Spinal Muscular Atrophy Type 1 (SMA1) in Europe
10.1055/s-0039-1698171
◽
2019
◽
Author(s):
Francesco Muntoni
◽
Giovanni Baranello
◽
Claudio Bruno
◽
Stefania Corti
◽
Riccardo Masson
◽
...
Keyword(s):
Spinal Muscular Atrophy
◽
Replacement Therapy
◽
Study Design
◽
Muscular Atrophy
◽
Gene Replacement
◽
Phase 3
◽
Spinal Muscular Atrophy Type
◽
Gene Replacement Therapy
Download Full-text
Gene-Replacement Therapy (GRT) in Spinal Muscular Atrophy Type 1 (SMA1): Long-Term Follow-Up From the Onasemnogene Abeparvovec Phase 1/2 Clinical Trial
10.1055/s-0039-1698259
◽
2019
◽
Cited By ~ 1
Author(s):
Jerry R. Mendell
◽
Richard Shell
◽
Kelly J. Lehman
◽
Markus McColly
◽
Linda P. Lowes
◽
...
Keyword(s):
Clinical Trial
◽
Muscular Atrophy
◽
Phase 1
◽
Gene Replacement
◽
Spinal Muscular Atrophy Type
◽
Gene Replacement Therapy
◽
Long Term Follow Up
Download Full-text
Sign in / Sign up
Close
Export Citation Format
Close
Share Document
Close