Leber Congenital Amaurosis gene therapy clinical trial
2009 ◽
Vol 9
(14)
◽
pp. 27-27
◽
W. W. Hauswirth
◽
A. V. Cideciyan
◽
T. S. Aleman
◽
S. Kaushal
◽
B. J. Byrne
◽
...
2016 ◽
Vol 95
(40)
◽
pp. e5110
◽
Shuo Yang
◽
Hong Yang
◽
Si-qi Ma
◽
Shuai-shuai Wang
◽
Heng He
◽
...
R. Shell
◽
S. Al-Zaidy
◽
W. Arnold
◽
L. Rodino-Klapac
◽
T. Prior
◽
...
2020 ◽
Vol 31
(19-20)
◽
pp. 1034-1042
Philip J. Brooks
◽
Elizabeth A. Ottinger
◽
Deanna Portero
◽
Richa Madan Lomash
◽
Asaf Alimardanov
◽
...
2017 ◽
Vol 21
◽
pp. e14
◽
Richard Shell
◽
Samiah Al-Zaidy
◽
W. Dave Arnold
◽
Louise Rodino-Klapac
◽
Thomas W. Prior
◽
...
Raman Mehrzad
◽
Paul Y. Liu
2014 ◽
Vol 25
(2)
◽
pp. 65-66
◽
2021 ◽
Vol 132
(2)
◽
pp. S56-S57
Jane Louise Kinsella
◽
Simon Jones
◽
Adrian J. Thrasher
◽
Claire Booth
◽
Karen F. Buckland
◽
...