`GENE THERAPY' FOR GAUCHER'S DISEASE SHOWS PROMISING RESULTS IN TEST ON MICE
Keyword(s):
University of Pittsburgh researchers reported promising results in mice with a potential "gene therapy" for Gaucher's disease that eventually may replace Ceredase, a Genzyme Corp. drug whose high cost has sparked controversy. The study indicated it would be possible to transfer a gene into certain cells of people with the disease that would permanently correct a genetic defect underlying their disorder. The potential treatment, however, is at least several years away from widespread use in patients, and its development may face economic stumbling blocks.
2011 ◽
Vol 5
(3)
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pp. 213-214
Keyword(s):
Isolation and characterization of a tartrate-sensitive splenic acid phosphatase in Gaucher's disease
1980 ◽
Vol 205
(1)
◽
pp. 156-168
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Keyword(s):
2006 ◽
Vol 17
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pp. S2-S5
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