Orphan designation: Recombinant adeno-associated viral vector containing a bioengineered capsid and a codon-optimised expression cassette to drive the expression of the SQ form of a B-domain deleted human coagulation factor VIII, Treatment of haemophilia A

2019 ◽  
Author(s):  
Keyword(s):  
Factor Viii ◽  
Viral Vector ◽  
Coagulation Factor ◽  
Expression Cassette ◽  
Coagulation Factor Viii ◽  
Haemophilia A ◽  
Orphan Designation

Promising coagulation factor VIII bypassing strategies for patients with haemophilia A

2014 ◽  
Vol 25 (6) ◽  
pp. 539-552 ◽  
Author(s):  
Xunwei Duan ◽  
Mingqing Tang ◽  
Junping Zhang ◽  
Hao Yu ◽  
Ruian Xu
Keyword(s):  
Factor Viii ◽  
Coagulation Factor ◽  
Coagulation Factor Viii ◽  
Haemophilia A

In silicoanalyses of missense mutations in coagulation factor VIII: identification of severity determinants of haemophilia A

Haemophilia ◽  
2015 ◽  
Vol 21 (5) ◽  
pp. 662-669 ◽  
Author(s):  
M. Sengupta ◽  
D. Sarkar ◽  
K. Ganguly ◽  
D. Sengupta ◽  
S. Bhaskar ◽  
...  
Keyword(s):  
Factor Viii ◽  
Coagulation Factor ◽  
Coagulation Factor Viii ◽  
Haemophilia A ◽  
Missense Mutations
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