Faculty Opinions recommendation of Systemic AAV9 gene therapy improves the lifespan of mice with Niemann-Pick disease, type C1.
2018 ◽
Vol 123
(2)
◽
pp. S36-S37
Cristin Davidson
◽
Alana Gibson
◽
Tansy Gu
◽
Randy Chandler
◽
Benjamin Deverman
◽
...
Randy J. Chandler
◽
Ian M. Williams
◽
Arturo A. Incao
◽
Forbes D. Porter
◽
William J. Pavan
◽
...
Yoshie Kurokawa
◽
Hitoshi Osaka
◽
Takeshi Kouga
◽
Eriko Jimbo
◽
Kazuhiro Muramatsu
◽
...
2021 ◽
Vol 32
(11-12)
◽
pp. 540-540
Randy J. Chandler
◽
Ian M. Williams
◽
Alana L. Gibson
◽
Cristin D. Davidson
◽
Arturo A. Incao
◽
...
Lydia Aston
◽
Rachel Shaw
◽
Rebecca Knibb
S Tay
◽
X He
◽
AM Jenner
◽
BS Wong
◽
WY Ong