scholarly journals Safety and Improved Efficacy Signals following Gene Therapy in Childhood Blindness Caused by GUCY2D Mutations

iScience ◽  
2021 ◽  
pp. 102409
Author(s):  
Samuel G. Jacobson ◽  
Artur V. Cideciyan ◽  
Allen C. Ho ◽  
Igor V. Peshenko ◽  
Alexandra V. Garafalo ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Childhood Blindness

Efficacy and safety of gene therapy with AAV4 in childhood blindness due to rpe65 mutations

2012 ◽  
Vol 90 ◽  
pp. 0-0 ◽  
Author(s):  
G LE MEUR ◽  
P LEBRANCHU ◽  
Y PEREON ◽  
F BILLAUD ◽  
C IVAN ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Efficacy And Safety ◽  
Childhood Blindness

Gene therapy restores vision in a canine model of childhood blindness

2001 ◽  
Vol 28 (1) ◽  
pp. 92-95 ◽  
Author(s):  
Gregory M. Acland ◽  
Gustavo D. Aguirre ◽  
Jharna Ray ◽  
Qi Zhang ◽  
Tomas S. Aleman ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Canine Model ◽  
Childhood Blindness

scholarly journals Improvement and Decline in Vision with Gene Therapy in Childhood Blindness

2015 ◽  
Vol 372 (20) ◽  
pp. 1920-1926 ◽  
Author(s):  
Samuel G. Jacobson ◽  
Artur V. Cideciyan ◽  
Alejandro J. Roman ◽  
Alexander Sumaroka ◽  
Sharon B. Schwartz ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Childhood Blindness

scholarly journals Gene therapy for inherited childhood blindness shows promise

2008 ◽  
Vol 3 (4) ◽  
pp. 357-359 ◽  
Author(s):  
James Bainbridge ◽  
Robin Ali
Keyword(s):  
Gene Therapy ◽  
Childhood Blindness
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