Gene therapy restores vision in a canine model of childhood blindness. Aceland GM, Aguirre GD, Ray J, Zang Q, Aleman TS, Cideciyan AV, Pearce-Kelling SE, Anand V, Zeng Y, Maguire AM, Jacobson SG, Hauswirth WW, Bennett J.∗∗FM Kirby Center, Scheie Eye Institute and Department of Ophthalmology, University of Pennsylvania, Philadelphia, PA. E-mail: jebennett@mail.med.upenn.edu Nat Gen 2001;28:92–95.

doi:10.1016/s0002-9394(01)01169-2

Gene therapy restores vision in a canine model of childhood blindness. Aceland GM, Aguirre GD, Ray J, Zang Q, Aleman TS, Cideciyan AV, Pearce-Kelling SE, Anand V, Zeng Y, Maguire AM, Jacobson SG, Hauswirth WW, Bennett J.∗∗FM Kirby Center, Scheie Eye Institute and Department of Ophthalmology, University of Pennsylvania, Philadelphia, PA. E-mail: [email protected] Nat Gen 2001;28:92–95.

American Journal of Ophthalmology ◽

10.1016/s0002-9394(01)01169-2 ◽

2001 ◽

Vol 132 (4) ◽

pp. 606

Keyword(s):

Gene Therapy ◽

Canine Model ◽

University Of Pennsylvania ◽

Childhood Blindness ◽

Department Of Ophthalmology ◽

E Mail

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Gene therapy restores vision in a canine model of childhood blindness

Nature Genetics ◽

10.1038/ng0501-92 ◽

2001 ◽

Vol 28 (1) ◽

pp. 92-95 ◽

Cited By ~ 407

Author(s):

Gregory M. Acland ◽

Gustavo D. Aguirre ◽

Jharna Ray ◽

Qi Zhang ◽

Tomas S. Aleman ◽

...

Keyword(s):

Gene Therapy ◽

Canine Model ◽

Childhood Blindness

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92. Safety and Histological Signs of Efficacy Following Systemic AAV9-CMV-Microutrophin Gene Therapy in a Canine Model for Duchenne Muscular Dystrophy

Molecular Therapy ◽

10.1016/s1525-0016(16)34427-6 ◽

2013 ◽

Vol 21 ◽

pp. S38

Keyword(s):

Gene Therapy ◽

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Canine Model

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Neonatal tolerance induction enables accurate evaluation of gene therapy for MPS I in a canine model

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2016.06.006 ◽

2016 ◽

Vol 119 (1-2) ◽

pp. 124-130 ◽

Cited By ~ 16

Author(s):

Christian Hinderer ◽

Peter Bell ◽

Jean-Pierre Louboutin ◽

Nathan Katz ◽

Yanqing Zhu ◽

...

Keyword(s):

Gene Therapy ◽

Tolerance Induction ◽

Canine Model ◽

Accurate Evaluation ◽

Mps I

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The resiliency of the corneal endothelium to refractive and intraocular surgery. Edelhauser HF.∗∗Department of Ophthalmology, Emory Eye Center, Suite B2600, 1365B Clifton Road NE, Atlanta, GA 30022. E-mail: [email protected] Cornea 2000;19:263–273.

American Journal of Ophthalmology ◽

10.1016/s0002-9394(00)00697-8 ◽

2000 ◽

Vol 130 (3) ◽

pp. 384 ◽

Cited By ~ 1

Keyword(s):

Corneal Endothelium ◽

Intraocular Surgery ◽

Department Of Ophthalmology ◽

E Mail

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Development of alternative gene transfer techniques for ex vivo and in vivo gene therapy in a canine model

Regenerative Therapy ◽

10.1016/j.reth.2021.08.009 ◽

2021 ◽

Vol 18 ◽

pp. 347-354

Author(s):

Masashi Noda ◽

Kohei Tatsumi ◽

Hideto Matsui ◽

Yasunori Matsunari ◽

Takeshi Sato ◽

...

Keyword(s):

Gene Therapy ◽

Gene Transfer ◽

Ex Vivo ◽

Canine Model ◽

Gene Transfer Techniques

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Dose Range Finding Studies with Two RPGR Transgenes in a Canine Model of X-Linked Retinitis Pigmentosa Treated with Subretinal Gene Therapy

Human Gene Therapy ◽

10.1089/hum.2019.337 ◽

2020 ◽

Vol 31 (13-14) ◽

pp. 743-755 ◽

Cited By ~ 1

Author(s):

Chunjuan Song ◽

Valérie L. Dufour ◽

Artur V. Cideciyan ◽

Guo-Jie Ye ◽

Malgorzata Swider ◽

...

Keyword(s):

Gene Therapy ◽

Retinitis Pigmentosa ◽

Dose Range ◽

Canine Model ◽

Range Finding

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Ex vivo gene therapy for the preservation of retinal and central nervous system structure and function in a canine model of CLN2 neuronal ceroid lipofuscinosis

10.32469/10355/56993 ◽

2016 ◽

Author(s):

Christopher J. Tracy

Keyword(s):

Gene Therapy ◽

Central Nervous System ◽

Nervous System ◽

Ex Vivo ◽

Neuronal Ceroid Lipofuscinosis ◽

Canine Model ◽

Structure And Function ◽

System Structure ◽

Ex Vivo Gene Therapy ◽

And Function

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Extraneuronal pathology in a canine model of CLN2 neuronal ceroid lipofuscinosis after intracerebroventricular gene therapy that delays neurological disease progression

Gene Therapy ◽

10.1038/gt.2017.4 ◽

2017 ◽

Vol 24 (4) ◽

pp. 215-223 ◽

Cited By ~ 22

Author(s):

M L Katz ◽

G C Johnson ◽

S B Leach ◽

B G Williamson ◽

J R Coates ◽

...

Keyword(s):

Gene Therapy ◽

Disease Progression ◽

Neurological Disease ◽

Neuronal Ceroid Lipofuscinosis ◽

Canine Model ◽

Ceroid Lipofuscinosis

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Retinal arteriolar narrowing and risk of coronary artery disease in men and women. The Atherosclerosis Risk in Communities Study.Wong TY,∗∗Department of Ophthalmology, National University of Singapore, 10 Kent Ridge Crescent, Singapore 119260. E-mail: [email protected]. Klein R, Sharrett AR, Duncan BB, Couper DJ, Tielsch JM, Klein BEK, Hubbard LD. JAMA 2002;287:1153–1159.

American Journal of Ophthalmology ◽

10.1016/s0002-9394(02)01485-x ◽

2002 ◽

Vol 133 (6) ◽

pp. 865

Author(s):

Nancy J. Newman

Keyword(s):

Coronary Artery Disease ◽

Men And Women ◽

Atherosclerosis Risk In Communities ◽

Department Of Ophthalmology ◽

Atherosclerosis Risk ◽

National University ◽

Artery Disease ◽

Arteriolar Narrowing ◽

E Mail ◽

Retinal Arteriolar

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Efficacy and safety of gene therapy with AAV4 in childhood blindness due to rpe65 mutations

Acta Ophthalmologica ◽

10.1111/j.1755-3768.2012.4223.x ◽

2012 ◽

Vol 90 ◽

pp. 0-0 ◽

Cited By ~ 3

Author(s):

G LE MEUR ◽

P LEBRANCHU ◽

Y PEREON ◽

F BILLAUD ◽

C IVAN ◽

...

Keyword(s):

Gene Therapy ◽

Efficacy And Safety ◽

Childhood Blindness

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