367 Phase I clinical trial for Recessive Dystrophic Epidermolysis Bullosa using genetically corrected autologous keratinocytes

Journal of Investigative Dermatology ◽

10.1016/j.jid.2016.02.400 ◽

2016 ◽

Vol 136 (5) ◽

pp. S65

Author(s):

Z. Siprashvili ◽

N.T. Nguyen ◽

E.S. Gorell ◽

K. Loutit ◽

P. Khuu ◽

...

Keyword(s):

Clinical Trial ◽

Phase I ◽

Epidermolysis Bullosa ◽

Phase I Clinical Trial ◽

Dystrophic Epidermolysis Bullosa ◽

Recessive Dystrophic Epidermolysis Bullosa

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519 Phase I/IIa clinical trial for recessive dystrophic epidermolysis bullosa using genetically corrected autologous keratinocytes

Journal of Investigative Dermatology ◽

10.1016/j.jid.2017.02.539 ◽

2017 ◽

Vol 137 (5) ◽

pp. S89 ◽

Author(s):

Z. Siprashvili ◽

N. Nguyen ◽

E. Gorell ◽

K. Loutit ◽

Y. Dutt-Singkh ◽

...

Keyword(s):

Clinical Trial ◽

Phase I ◽

Epidermolysis Bullosa ◽

Dystrophic Epidermolysis Bullosa ◽

Recessive Dystrophic Epidermolysis Bullosa

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Phase I/II Ex Vivo Gene Therapy Clinical Trial for Recessive Dystrophic Epidermolysis Bullosa Using Skin Equivalent Grafts Genetically Corrected with a COL7A1-Encoding SIN Retroviral Vector (GENEGRAFT)

Human Gene Therapy Clinical Development ◽

10.1089/humc.2014.2508 ◽

2014 ◽

Vol 25 (2) ◽

pp. 65-66 ◽

Keyword(s):

Clinical Trial ◽

Gene Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Retroviral Vector ◽

Dystrophic Epidermolysis Bullosa ◽

Ex Vivo Gene Therapy ◽

Recessive Dystrophic Epidermolysis Bullosa ◽

Therapy Clinical Trial

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725. Correction of Laminin-5-Deficient Junctional Epidermolysis Bullosa by Transplantation of Genetically Modified Epidermal Stem Cells. A Phase-I Clinical Trial

Molecular Therapy ◽

10.1016/j.ymthe.2006.08.805 ◽

2006 ◽

Vol 13 ◽

pp. S280

Author(s):

Fulvio Mavilio ◽

Stefano Ferrari ◽

Francesca Di Nunzio ◽

Giulietta Maruggi ◽

Chiara Bonini ◽

...

Keyword(s):

Clinical Trial ◽

Phase I ◽

Epidermolysis Bullosa ◽

Genetically Modified ◽

Phase I Clinical Trial ◽

Epidermal Stem Cells ◽

Junctional Epidermolysis Bullosa ◽

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Patient pre-selection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa.

10.26226/morressier.595a9c56d462b80296c9fadf ◽

2017 ◽

Author(s):

Su Lwin

Keyword(s):

Gene Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Dystrophic Epidermolysis Bullosa ◽

Gene Therapy Trial ◽

Recessive Dystrophic Epidermolysis Bullosa ◽

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Phase 3, Open-label Clinical Trial of EB-101 for the Treatment of Recessive Dystrophic Epidermolysis Bullosa (RDEB)

Case Medical Research ◽

10.31525/ct1-nct04227106 ◽

2020 ◽

Author(s):

Keyword(s):

Clinical Trial ◽

Epidermolysis Bullosa ◽

Phase 3 ◽

Dystrophic Epidermolysis Bullosa ◽

Recessive Dystrophic Epidermolysis Bullosa

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EBGene trial: patient preselection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa

British Journal of Dermatology ◽

10.1111/bjd.18559 ◽

2019 ◽

Vol 182 (3) ◽

pp. 794-797 ◽

Author(s):

S. Gaucher ◽

S.M. Lwin ◽

M. Titeux ◽

A. Abdul‐Wahab ◽

N. Pironon ◽

...

Keyword(s):

Gene Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Dystrophic Epidermolysis Bullosa ◽

Gene Therapy Trial ◽

Recessive Dystrophic Epidermolysis Bullosa ◽

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732. Lentiviral-Mediated COL7A1 Gene Modified Autologous Fibroblast Therapy for Recessive Dystrophic Epidermolysis Bullosa (RDEB): Preparations for Phase-I Clinical Trials

Molecular Therapy ◽

10.1016/s1525-0016(16)35745-8 ◽

2014 ◽

Vol 22 ◽

pp. S283

Keyword(s):

Clinical Trials ◽

Phase I ◽

Epidermolysis Bullosa ◽

Phase I Clinical Trials ◽

Dystrophic Epidermolysis Bullosa ◽

Recessive Dystrophic Epidermolysis Bullosa ◽

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Phase I/II open-label trial of intravenous allogeneic mesenchymal stromal cell therapy in adults with recessive dystrophic epidermolysis bullosa

Journal of the American Academy of Dermatology ◽

10.1016/j.jaad.2019.11.038 ◽

2020 ◽

Vol 83 (2) ◽

pp. 447-454 ◽

Author(s):

Ellie Rashidghamat ◽

Tendai Kadiyirire ◽

Salma Ayis ◽

Gabriela Petrof ◽

Lu Liu ◽

...

Keyword(s):

Cell Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Mesenchymal Stromal Cell ◽

Stromal Cell ◽

Dystrophic Epidermolysis Bullosa ◽

Recessive Dystrophic Epidermolysis Bullosa ◽

Open Label Trial

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227 Patient pre-selection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa

Journal of Investigative Dermatology ◽

10.1016/j.jid.2017.07.224 ◽

2017 ◽

Vol 137 (10) ◽

pp. S231

Author(s):

S.M. Lwin ◽

S. Gaucher ◽

M. Titeux ◽

A. Abdul-Wahab ◽

N. Pironon ◽

...

Keyword(s):

Gene Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Dystrophic Epidermolysis Bullosa ◽

Gene Therapy Trial ◽

Recessive Dystrophic Epidermolysis Bullosa ◽

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Clinical trial of ABCB5-positive mesenchymal stem cells for recessive dystrophic epidermolysis bullosa

JCI Insight ◽

10.1172/jci.insight.151922 ◽

2021 ◽

Author(s):

Dimitra Kiritsi ◽

Kathrin Dieter ◽

Elke Niebergall-Roth ◽

Silvia Fluhr ◽

Cristina Daniele ◽

...

Keyword(s):

Clinical Trial ◽

Mesenchymal Stem Cells ◽

Epidermolysis Bullosa ◽

Dystrophic Epidermolysis Bullosa ◽

Recessive Dystrophic Epidermolysis Bullosa

Download Full-text