P3.55 CRIM status and antibody formation in patients with classic infantile Pompe disease treated with enzyme-replacement therapy

2011 ◽  
Vol 21 (9-10) ◽  
pp. 699
Author(s):  
C.M. van Gelder ◽  
M.A. Kroos ◽  
L. Ozkan ◽  
A.T. van der Ploeg ◽  
A.J. Reuser
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Pompe Disease ◽  
Antibody Formation ◽  
Enzyme Replacement ◽  
Crim Status ◽  
Infantile Pompe Disease

Antibody formation to enzyme replacement therapy in classic infantile Pompe disease: effects of immunomodulation in naïve patients

2017 ◽  
Vol 27 ◽  
pp. S162
Author(s):  
E. Poelman ◽  
M. Hoogeveen–Westerveld ◽  
M. Kroos-de Haan ◽  
J. van den Hout ◽  
K. Bronsema ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Pompe Disease ◽  
Antibody Formation ◽  
Enzyme Replacement ◽  
Infantile Pompe Disease

scholarly journals Pulmonary outcome measures in long‐term survivors of infantile Pompe disease on enzyme replacement therapy: A case series

2020 ◽  
Vol 55 (3) ◽  
pp. 674-681
Author(s):  
Mai K. ElMallah ◽  
Ankit K. Desai ◽  
Erica B. Nading ◽  
Stephanie DeArmey ◽  
Richard M. Kravitz ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Outcome Measures ◽  
Pompe Disease ◽  
Case Series ◽  
Enzyme Replacement ◽  
Infantile Pompe Disease ◽  
Long Term Survivors

Pompe disease in adulthood: effects of antibody formation on enzyme replacement therapy

2016 ◽  
Vol 19 (1) ◽  
pp. 90-97 ◽  
Author(s):  
Juna M. de Vries ◽  
Esther Kuperus ◽  
Marianne Hoogeveen-Westerveld ◽  
Marian A. Kroos ◽  
Stephan C.A. Wens ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Pompe Disease ◽  
Antibody Formation ◽  
Enzyme Replacement

scholarly journals Motor Development as a Potential Marker to Monitor Infantile Pompe Disease on Enzyme Replacement Therapy

2017 ◽  
Vol 07 (01) ◽  
pp. 8-19 ◽  
Author(s):  
Paula de Almeida Thomazinho ◽  
Fernanda Bertão Scalco ◽  
Maria Lúcia Costa de Oliveira ◽  
Dafne Dain Gandelman Horovitz ◽  
Juan Clinton Llerena Jr.
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Motor Development ◽  
Pompe Disease ◽  
Enzyme Replacement ◽  
Potential Marker ◽  
Infantile Pompe Disease

scholarly journals Ocular and Histologic Findings in a Series of Children With Infantile Pompe Disease Treated With Enzyme Replacement Therapy

2014 ◽  
Vol 51 (6) ◽  
pp. 355-362 ◽  
Author(s):  
S. Grace Prakalapakorn ◽  
Alan D. Proia ◽  
Tammy L. Yanovitch ◽  
Stephanie DeArmey ◽  
Nancy J. Mendelsohn ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Pompe Disease ◽  
Enzyme Replacement ◽  
Infantile Pompe Disease

When Should We Start Enzyme Replacement Therapy for Infantile Pompe Disease With Severe Cardiomyopathy?

2012 ◽  
Vol 65 (1) ◽  
pp. 100-102
Author(s):  
Juan L. Bonilla-Palomas ◽  
Antonio L. Gámez-López ◽  
María A. Tejero-Hernández ◽  
Ignacio Tejero-Mateo ◽  
Juana López-López
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Pompe Disease ◽  
Enzyme Replacement ◽  
Infantile Pompe Disease
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