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Liver-Targeted AAV8 Gene Therapy Ameliorates Skeletal and Cardiovascular Pathology in a Mucopolysaccharidosis IVA Murine Model
Molecular Therapy — Methods & Clinical Development
◽
10.1016/j.omtm.2020.05.015
◽
2020
◽
Vol 18
◽
pp. 50-61
Author(s):
Kazuki Sawamoto
◽
Subha Karumuthil-Melethil
◽
Shaukat Khan
◽
Molly Stapleton
◽
Joseph T. Bruder
◽
...
Keyword(s):
Gene Therapy
◽
Murine Model
◽
Cardiovascular Pathology
◽
Mucopolysaccharidosis Iva
Download Full-text
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Gene Therapy for a Murine Model of Eosinophilic Esophagitis
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10.1111/all.14822
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2021
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Saparja Nag
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Anthony R. Russo
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Ronald G. Crystal
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Impact of PEDF gene therapy delivered by AAV8 in murine model of chronic allergic inflammation
Cytotherapy
◽
10.1016/s1465324921005338
◽
2021
◽
Vol 23
(5)
◽
pp. S153
Author(s):
D.P. Ferreira
Keyword(s):
Gene Therapy
◽
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◽
Allergic Inflammation
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P0563 : RNAi-based gene therapy for chronic hepatitis B: Evaluation in a murine model
Journal of Hepatology
◽
10.1016/s0168-8278(15)30770-4
◽
2015
◽
Vol 62
◽
pp. S526
Author(s):
T. Michler
◽
S. Grosse
◽
S. Mockenhaupt
◽
M. Heikenwaelder
◽
D. Grimm
◽
...
Keyword(s):
Gene Therapy
◽
Chronic Hepatitis
◽
Hepatitis B
◽
Chronic Hepatitis B
◽
Murine Model
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69. Gene therapy of mucopolysaccharidosis type I: Intraventricular administration of adeno-associated virus vector transducing the human alpha-l-iduronidase gene in a murine model of the disease
Molecular Genetics and Metabolism
◽
10.1016/j.ymgme.2007.10.081
◽
2008
◽
Vol 93
(2)
◽
pp. 31
Author(s):
R. Scott McIvor
◽
Daniel A. Wolf
◽
Zhenhong Nan
◽
Mayra Quito
◽
Kelly Podetz-Pedersen
◽
...
Keyword(s):
Gene Therapy
◽
Murine Model
◽
Virus Vector
◽
Type I
◽
Intraventricular Administration
◽
Mucopolysaccharidosis Type
◽
Mucopolysaccharidosis Type I
◽
Adeno Associated Virus
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CaSm/gemcitabine chemo-gene therapy leads to prolonged survival in a murine model of pancreatic cancer
Surgery
◽
10.1067/msy.2001.115899
◽
2001
◽
Vol 130
(2)
◽
pp. 280-288
◽
Cited By ~ 11
Author(s):
Joseph R. Kelley
◽
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◽
Clifford W. Schweinfest
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Pancreatic Cancer
◽
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Prolonged Survival
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Replacement Gene Therapy with a HumanRPGRIP1Sequence Slows Photoreceptor Degeneration in a Murine Model of Leber Congenital Amaurosis
Human Gene Therapy
◽
10.1089/hum.2009.218
◽
2010
◽
Vol 21
(8)
◽
pp. 993-1004
◽
Cited By ~ 49
Author(s):
Basil S. Pawlyk
◽
Oleg V. Bulgakov
◽
Xiaoqing Liu
◽
Xiaoyun Xu
◽
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...
Keyword(s):
Gene Therapy
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Murine Model
◽
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◽
Leber Congenital Amaurosis
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Erratum: Hepatocytes corrected by gene therapy are selected in vivo in a murine model of hereditary tyrosinaemia type I
Nature Genetics
◽
10.1038/ng0496-458a
◽
1996
◽
Vol 12
(4)
◽
pp. 458-458
◽
Cited By ~ 1
Keyword(s):
Gene Therapy
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Murine Model
◽
Type I
◽
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207. In Vivo Assessment of the Efficacy of Gene Therapy Targeted to Diseased Human Hematopoietic Progenitor Cells in a Xenotransplantable Murine Model of a Lysosomal Storage Disorder
Molecular Therapy
◽
10.1016/s1525-0016(16)40649-0
◽
2003
◽
Vol 7
(5)
◽
pp. S81-S82
◽
Cited By ~ 1
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◽
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◽
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◽
Lysosomal Storage Disorder
◽
Hematopoietic Progenitor Cells
◽
Lysosomal Storage
◽
Hematopoietic Progenitor
◽
Storage Disorder
◽
In Vivo Assessment
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404. Long-Term Rescue of a Lethal Murine Model of Methylmalonic Acidemia Using AAV 8 Mediated Gene Therapy
Molecular Therapy
◽
10.1016/s1525-0016(16)39807-0
◽
2008
◽
Vol 16
◽
pp. S153
Keyword(s):
Gene Therapy
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Methylmalonic Acidemia
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Abstract 4772: Evaluation of immune response following ultrasound targeted gene therapy in a murine model of prostate cancer
10.1158/1538-7445.sabcs18-4772
◽
2019
◽
Author(s):
Flavia De Carlo
◽
Elliot T. Varney
◽
Pier Paolo Claudio
◽
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Keyword(s):
Prostate Cancer
◽
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◽
Immune Response
◽
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◽
Targeted Gene Therapy
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