scholarly journals Liver-Targeted AAV8 Gene Therapy Ameliorates Skeletal and Cardiovascular Pathology in a Mucopolysaccharidosis IVA Murine Model

2020 ◽  
Vol 18 ◽  
pp. 50-61
Author(s):  
Kazuki Sawamoto ◽  
Subha Karumuthil-Melethil ◽  
Shaukat Khan ◽  
Molly Stapleton ◽  
Joseph T. Bruder ◽  
...  
Allergy ◽  
2021 ◽  
Author(s):  
Anna E. Camilleri ◽  
Saparja Nag ◽  
Anthony R. Russo ◽  
Katie M. Stiles ◽  
Ronald G. Crystal ◽  
...  

2015 ◽  
Vol 62 ◽  
pp. S526
Author(s):  
T. Michler ◽  
S. Grosse ◽  
S. Mockenhaupt ◽  
M. Heikenwaelder ◽  
D. Grimm ◽  
...  

Surgery ◽  
2001 ◽  
Vol 130 (2) ◽  
pp. 280-288 ◽  
Author(s):  
Joseph R. Kelley ◽  
Melissa M. Fraser ◽  
Clifford W. Schweinfest ◽  
John N. Vournakis ◽  
Dennis K. Watson ◽  
...  

2010 ◽  
Vol 21 (8) ◽  
pp. 993-1004 ◽  
Author(s):  
Basil S. Pawlyk ◽  
Oleg V. Bulgakov ◽  
Xiaoqing Liu ◽  
Xiaoyun Xu ◽  
Michael Adamian ◽  
...  

Sign in / Sign up

Export Citation Format

Share Document