69. Gene therapy of mucopolysaccharidosis type I: Intraventricular administration of adeno-associated virus vector transducing the human alpha-l-iduronidase gene in a murine model of the disease

2008 ◽  
Vol 93 (2) ◽  
pp. 31
Author(s):  
R. Scott McIvor ◽  
Daniel A. Wolf ◽  
Zhenhong Nan ◽  
Mayra Quito ◽  
Kelly Podetz-Pedersen ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Murine Model ◽  
Virus Vector ◽  
Type I ◽  
Intraventricular Administration ◽  
Mucopolysaccharidosis Type ◽  
Mucopolysaccharidosis Type I ◽  
Adeno Associated Virus

11 Adeno-associated virus vector-mediated gene therapy in a murine model of mucopolysaccharidosis type I

2007 ◽  
Vol 92 (4) ◽  
pp. 13-14
Author(s):  
Lalitha Belur ◽  
Zachary deMorest ◽  
Chester B. Whitley ◽  
Walter C. Low ◽  
R. Scott McIvor
Keyword(s):  
Gene Therapy ◽  
Murine Model ◽  
Virus Vector ◽  
Type I ◽  
Mucopolysaccharidosis Type ◽  
Mucopolysaccharidosis Type I ◽  
Adeno Associated Virus

Gene Therapy for a Mucopolysaccharidosis Type I Murine Model with Lentiviral-IDUA Vector

2005 ◽  
Vol 16 (1) ◽  
pp. 81-90 ◽  
Author(s):  
Carmela Di Domenico ◽  
Guglielmo R.D. Villani ◽  
Daniele Di Napoli ◽  
Enrico Gonzalez Y Reyero ◽  
Angelo Lombardo ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Murine Model ◽  
Type I ◽  
Mucopolysaccharidosis Type ◽  
Mucopolysaccharidosis Type I

scholarly journals Sexual behaviour in a murine model of mucopolysaccharidosis type I (MPS I)

PLoS ONE ◽  
2019 ◽  
Vol 14 (12) ◽  
pp. e0220429 ◽  
Author(s):  
Ana Barbosa Mendes ◽  
Cinthia Castro do Nascimento ◽  
Vânia D’Almeida
Keyword(s):  
Sexual Behaviour ◽  
Murine Model ◽  
Type I ◽  
Mucopolysaccharidosis Type ◽  
Mucopolysaccharidosis Type I ◽  
Mps I

scholarly journals Liver-directed gene therapy corrects cardiovascular lesions in feline mucopolysaccharidosis type I

2014 ◽  
Vol 111 (41) ◽  
pp. 14894-14899 ◽  
Author(s):  
C. Hinderer ◽  
P. Bell ◽  
B. L. Gurda ◽  
Q. Wang ◽  
J.-P. Louboutin ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Type I ◽  
Mucopolysaccharidosis Type ◽  
Mucopolysaccharidosis Type I

scholarly journals Characterization of an immunodeficient mouse model of mucopolysaccharidosis type I suitable for preclinical testing of human stem cell and gene therapy

2007 ◽  
Vol 74 (6) ◽  
pp. 429-438 ◽  
Author(s):  
Mayra F. Garcia-Rivera ◽  
Leah E. Colvin-Wanshura ◽  
Matthew S. Nelson ◽  
Zhenhong Nan ◽  
Shaukat A. Khan ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Mouse Model ◽  
Type I ◽  
Mucopolysaccharidosis Type ◽  
Mucopolysaccharidosis Type I ◽  
Human Stem Cell ◽  
Preclinical Testing ◽  
Cell And Gene Therapy
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