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Real-time MR tracking of AAV gene therapy with βgal-responsive MR probe in a murine model of GM1-gangliosidosis
Molecular Therapy — Methods & Clinical Development
◽
10.1016/j.omtm.2021.08.003
◽
2021
◽
Vol 23
◽
pp. 128-134
Author(s):
Toloo Taghian
◽
Ana Rita Batista
◽
Sarah Kamper
◽
Michael Caldwell
◽
Laura Lilley
◽
...
Keyword(s):
Gene Therapy
◽
Real Time
◽
Murine Model
◽
Gm1 Gangliosidosis
Download Full-text
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Gene Therapy for a Murine Model of Eosinophilic Esophagitis
Allergy
◽
10.1111/all.14822
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2021
◽
Author(s):
Anna E. Camilleri
◽
Saparja Nag
◽
Anthony R. Russo
◽
Katie M. Stiles
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Ronald G. Crystal
◽
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Gene Therapy
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◽
Murine Model
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Examination of a blood-brain barrier targeting β-galactosidase-monoclonal antibody fusion protein in a murine model of GM1-gangliosidosis
Molecular Genetics and Metabolism
◽
10.1016/j.ymgme.2020.12.210
◽
2021
◽
Vol 132
(2)
◽
pp. S88
Author(s):
Michael Przybilla
◽
Christine Stewart
◽
Timothy Carlson
◽
Li Ou
◽
Brenda Koniar
◽
...
Keyword(s):
Monoclonal Antibody
◽
Fusion Protein
◽
Blood Brain Barrier
◽
Murine Model
◽
Brain Barrier
◽
Gm1 Gangliosidosis
◽
Blood Brain
◽
Antibody Fusion Protein
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Impact of PEDF gene therapy delivered by AAV8 in murine model of chronic allergic inflammation
Cytotherapy
◽
10.1016/s1465324921005338
◽
2021
◽
Vol 23
(5)
◽
pp. S153
Author(s):
D.P. Ferreira
Keyword(s):
Gene Therapy
◽
Murine Model
◽
Allergic Inflammation
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Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model
Molecular Therapy
◽
10.1016/j.ymthe.2017.01.009
◽
2017
◽
Vol 25
(4)
◽
pp. 892-903
◽
Cited By ~ 11
Author(s):
Heather L. Gray-Edwards
◽
Debra S. Regier
◽
Jamie L. Shirley
◽
Ashley N. Randle
◽
Nouha Salibi
◽
...
Keyword(s):
Gene Therapy
◽
Clinical Efficacy
◽
Gm1 Gangliosidosis
◽
Novel Biomarkers
◽
Feline Model
Download Full-text
P0563 : RNAi-based gene therapy for chronic hepatitis B: Evaluation in a murine model
Journal of Hepatology
◽
10.1016/s0168-8278(15)30770-4
◽
2015
◽
Vol 62
◽
pp. S526
Author(s):
T. Michler
◽
S. Grosse
◽
S. Mockenhaupt
◽
M. Heikenwaelder
◽
D. Grimm
◽
...
Keyword(s):
Gene Therapy
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Chronic Hepatitis
◽
Hepatitis B
◽
Chronic Hepatitis B
◽
Murine Model
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69. Gene therapy of mucopolysaccharidosis type I: Intraventricular administration of adeno-associated virus vector transducing the human alpha-l-iduronidase gene in a murine model of the disease
Molecular Genetics and Metabolism
◽
10.1016/j.ymgme.2007.10.081
◽
2008
◽
Vol 93
(2)
◽
pp. 31
Author(s):
R. Scott McIvor
◽
Daniel A. Wolf
◽
Zhenhong Nan
◽
Mayra Quito
◽
Kelly Podetz-Pedersen
◽
...
Keyword(s):
Gene Therapy
◽
Murine Model
◽
Virus Vector
◽
Type I
◽
Intraventricular Administration
◽
Mucopolysaccharidosis Type
◽
Mucopolysaccharidosis Type I
◽
Adeno Associated Virus
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CaSm/gemcitabine chemo-gene therapy leads to prolonged survival in a murine model of pancreatic cancer
Surgery
◽
10.1067/msy.2001.115899
◽
2001
◽
Vol 130
(2)
◽
pp. 280-288
◽
Cited By ~ 11
Author(s):
Joseph R. Kelley
◽
Melissa M. Fraser
◽
Clifford W. Schweinfest
◽
John N. Vournakis
◽
Dennis K. Watson
◽
...
Keyword(s):
Pancreatic Cancer
◽
Gene Therapy
◽
Murine Model
◽
Prolonged Survival
Download Full-text
Replacement Gene Therapy with a HumanRPGRIP1Sequence Slows Photoreceptor Degeneration in a Murine Model of Leber Congenital Amaurosis
Human Gene Therapy
◽
10.1089/hum.2009.218
◽
2010
◽
Vol 21
(8)
◽
pp. 993-1004
◽
Cited By ~ 49
Author(s):
Basil S. Pawlyk
◽
Oleg V. Bulgakov
◽
Xiaoqing Liu
◽
Xiaoyun Xu
◽
Michael Adamian
◽
...
Keyword(s):
Gene Therapy
◽
Murine Model
◽
Photoreceptor Degeneration
◽
Leber Congenital Amaurosis
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114. AAV-Mediated Gene Therapy Reduces Glycosphingolipid Storage in Adult GM1 Gangliosidosis Mice
Molecular Therapy
◽
10.1016/s1525-0016(16)39517-x
◽
2008
◽
Vol 16
◽
pp. S44
Keyword(s):
Gene Therapy
◽
Gm1 Gangliosidosis
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Erratum: Hepatocytes corrected by gene therapy are selected in vivo in a murine model of hereditary tyrosinaemia type I
Nature Genetics
◽
10.1038/ng0496-458a
◽
1996
◽
Vol 12
(4)
◽
pp. 458-458
◽
Cited By ~ 1
Keyword(s):
Gene Therapy
◽
Murine Model
◽
Type I
◽
Tyrosinaemia Type
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