Causes of Death (COD) in 184 Patients With Type 1 Gaucher Disease (GD1) from the United States Who Were Never Treated With Enzyme Replacement Therapy (ERT)

Replacement Therapy ◽

Gaucher Disease ◽

Causes Of Death ◽

The United States ◽

Enzyme Replacement ◽

Causes of death in 184 patients with type 1 Gaucher disease from the United States who were never treated with enzyme replacement therapy

Blood Cells Molecules and Diseases ◽

10.1016/j.bcmd.2016.10.002 ◽

2018 ◽

Vol 68 ◽

pp. 211-217 ◽

Cited By ~ 18

Author(s):

Neal J Weinreb ◽

Deborah S Barbouth ◽

Robert E Lee

Keyword(s):

United States ◽

Replacement Therapy ◽

Gaucher Disease ◽

Causes Of Death ◽

The United States ◽

Enzyme Replacement ◽

Causes of Death Due to Hematological and Non-Hematological Cancers in 57 US Patients with Type 1 Gaucher Disease Who Were Never Treated with Enzyme Replacement Therapy

Critical Reviews in Oncogenesis ◽

10.1615/critrevoncog.2013005921 ◽

2013 ◽

Vol 18 (3) ◽

pp. 177-195 ◽

Cited By ~ 25

Author(s):

Neal J. Weinreb ◽

Robert E. Lee

Keyword(s):

Replacement Therapy ◽

Gaucher Disease ◽

Causes Of Death ◽

Enzyme Replacement ◽

Hematological Cancers ◽

A pharmacokinetic analysis of a novel enzyme replacement therapy with Gene-Activated® human glucocerebrosidase (GA-GCB) in patients with type 1 Gaucher disease

Blood Cells Molecules and Diseases ◽

10.1016/j.bcmd.2007.02.008 ◽

2007 ◽

Vol 39 (1) ◽

pp. 115-118 ◽

Cited By ~ 46

Author(s):

Ari Zimran ◽

Kenneth Loveday ◽

Candida Fratazzi ◽

Deborah Elstein

Keyword(s):

Replacement Therapy ◽

Gaucher Disease ◽

Pharmacokinetic Analysis ◽

Enzyme Replacement ◽

156. Enzyme replacement therapy with velaglucerase alfa improves key clinical parameters in a pediatric subgroup with type 1 Gaucher disease

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2009.10.173 ◽

2010 ◽

Vol 99 (2) ◽

pp. S40-S41 ◽

Cited By ~ 1

Author(s):

Ari Zimran ◽

Derlis Gonzalez ◽

Eric Crombez ◽

Kiran Bhirangi

Keyword(s):

Replacement Therapy ◽

Gaucher Disease ◽

Clinical Parameters ◽

Enzyme Replacement ◽

Effectiveness of enzyme replacement therapy in 1028 patients with type 1 Gaucher disease after 2 to 5 years of treatment: a report from the Gaucher Registry

The American Journal of Medicine ◽

10.1016/s0002-9343(02)01150-6 ◽

2002 ◽

Vol 113 (2) ◽

pp. 112-119 ◽

Cited By ~ 365

Author(s):

Neal J Weinreb ◽

Joel Charrow ◽

Hans C Andersson ◽

Paige Kaplan ◽

Edwin H Kolodny ◽

...

Keyword(s):

Replacement Therapy ◽

Gaucher Disease ◽

Enzyme Replacement ◽

Acute lymphoblastic leukemia in a patient with type 1 Gaucher disease developing 1 year after discontinuation of enzyme replacement therapy

American Journal of Hematology ◽

10.1002/ajh.21839 ◽

2010 ◽

Vol 85 (11) ◽

pp. 908-909 ◽

Cited By ~ 2

Author(s):

Aditi Ranade ◽

Sorin Selegean ◽

Gagangeet Sandhu ◽

Violette Ghali ◽

Vijay P. Shah

Keyword(s):

Acute Lymphoblastic Leukemia ◽

Replacement Therapy ◽

Gaucher Disease ◽

Lymphoblastic Leukemia ◽

Enzyme Replacement ◽

Persistent bone disease in adult type 1 Gaucher disease despite increasing doses of enzyme replacement therapy

Haematologica ◽

10.3324/haematol.12651 ◽

2008 ◽

Vol 93 (7) ◽

pp. 1119-1120 ◽

Cited By ~ 36

Author(s):

M. de Fost ◽

C. J.M. van Noesel ◽

J. M.F.G. Aerts ◽

M. Maas ◽

R. G. Poll ◽

...

Keyword(s):

Replacement Therapy ◽

Bone Disease ◽

Gaucher Disease ◽

Adult Type ◽

Enzyme Replacement ◽

Cost-effectiveness of enzyme replacement therapy for type 1 Gaucher disease

Orphanet Journal of Rare Diseases ◽

10.1186/1750-1172-9-51 ◽

2014 ◽

Vol 9 (1) ◽

pp. 51 ◽

Cited By ~ 27

Author(s):

Laura van Dussen ◽

Marieke Biegstraaten ◽

Carla EM Hollak ◽

Marcel GW Dijkgraaf

Keyword(s):

Cost Effectiveness ◽

Replacement Therapy ◽

Gaucher Disease ◽

Enzyme Replacement ◽

Improvement of Splenomegaly and Pancytopenia by Enzyme Replacement Therapy Against Type 1 Gaucher Disease: A Report of Sibling Cases

International Journal of Hematology ◽

10.1007/bf02981962 ◽

2001 ◽

Vol 73 (3) ◽

pp. 356-362

Author(s):

Kazuya Tsuboi ◽

Shinsuke Iida ◽

Miyuki Kato ◽

Yoshihito Hayami ◽

Ichiro Hanamura ◽

...

Keyword(s):

Replacement Therapy ◽

Gaucher Disease ◽

Enzyme Replacement ◽

Type 1 Gaucher Disease ◽

Sibling Cases

Regression of skeletal changes in type 1 Gaucher disease with enzyme replacement therapy

Skeletal Radiology ◽

10.1007/s002560050120 ◽

1996 ◽

Vol 25 (5) ◽

pp. 485-488 ◽

Cited By ~ 18

Author(s):

Gregory M. Pastores ◽

G. Hermann ◽

Karen I. Norton ◽

Mordechai Lorberboym ◽

Robert J. Desnick

Keyword(s):

Replacement Therapy ◽

Gaucher Disease ◽

Enzyme Replacement ◽

Skeletal Changes ◽