A multi-national, randomized, double-blind, placebo-controlled study to evaluate the efficacy and safety of BMN 110 treatment for mucopolysaccharidosis IVA (Morquio syndrome type A)

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pp. S48 ◽  
Author(s):  
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Barbara K. Burton ◽  
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2005 ◽  
Vol 20 (7) ◽  
pp. 783-791 ◽  
Author(s):  
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Carlos Singer ◽  
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...  

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