Clinical outcomes in Morquio syndrome type A treated with elosulfase alfa: results from the managed access agreement in England
2018 ◽
Vol 123
(2)
◽
pp. S67
Derralynn Hughes
◽
Maureen Cleary
◽
Tarekegn Geberhiwot
◽
Christian J. Hendriksz
◽
Simon A. Jones
◽
...