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Impact of elosulfase alfa in patients with Morquio syndrome type A who have limited ambulation: An open-label, phase 2 study
Molecular Genetics and Metabolism
◽
10.1016/j.ymgme.2015.12.284
◽
2016
◽
Vol 117
(2)
◽
pp. S55
Author(s):
Paul R. Harmatz
◽
Andrea Jester
◽
Eugen Mengel
◽
Marsha Treadwell
◽
Barbara K. Burton
◽
...
Keyword(s):
Type A
◽
Syndrome Type
◽
Phase 2
◽
Open Label
◽
Phase 2 Study
◽
Open Label Phase
◽
Morquio Syndrome
◽
Elosulfase Alfa
Download Full-text
Related Documents
Cited By
References
Impact of elosulfase alfa in patients with morquio A syndrome who have limited ambulation: An open-label, phase 2 study
American Journal of Medical Genetics Part A
◽
10.1002/ajmg.a.38014
◽
2016
◽
Vol 173
(2)
◽
pp. 375-383
◽
Cited By ~ 12
Author(s):
Paul R. Harmatz
◽
Eugen Mengel
◽
Tarekegn Geberhiwot
◽
Nicole Muschol
◽
Christian J. Hendriksz
◽
...
Keyword(s):
Phase 2
◽
Open Label
◽
Morquio A
◽
Phase 2 Study
◽
Open Label Phase
◽
Morquio A Syndrome
◽
Elosulfase Alfa
Download Full-text
Safety, efficacy, and immunogenicity of elosulfase alfa in patients with Morquio syndrome type A participating in 2 sequential open-label studies (MOR-002/MOR-100), representing 5 years of treatment
Molecular Genetics and Metabolism
◽
10.1016/j.ymgme.2017.12.148
◽
2018
◽
Vol 123
(2)
◽
pp. S61
Author(s):
Christian Hendriksz
◽
Saikat Santra
◽
Simon A. Jones
◽
Tarekegn Geberhiwot
◽
Lynne Jesaitis
◽
...
Keyword(s):
Type A
◽
Syndrome Type
◽
Open Label
◽
Morquio Syndrome
◽
Elosulfase Alfa
Download Full-text
Faculty Opinions recommendation of An open-label, phase 2 study evaluating the efficacy and safety of the anti-IGF-1R antibody cixutumumab in patients with previously treated advanced or metastatic soft-tissue sarcoma or Ewing family of tumours.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.718028323.793480222
◽
2013
◽
Author(s):
Richard Riedel
Keyword(s):
Soft Tissue
◽
Soft Tissue Sarcoma
◽
Phase 2
◽
Efficacy And Safety
◽
Open Label
◽
Phase 2 Study
◽
Open Label Phase
◽
Metastatic Soft Tissue Sarcoma
◽
Previously Treated
Download Full-text
Belantamab mafodotin for relapsed or refractory multiple myeloma (DREAMM-2): a two-arm, randomised, open-label, phase 2 study
The Lancet Oncology
◽
10.1016/s1470-2045(19)30788-0
◽
2020
◽
Vol 21
(2)
◽
pp. 207-221
◽
Cited By ~ 72
Author(s):
Sagar Lonial
◽
Hans C Lee
◽
Ashraf Badros
◽
Suzanne Trudel
◽
Ajay K Nooka
◽
...
Keyword(s):
Multiple Myeloma
◽
Phase 2
◽
Open Label
◽
Refractory Multiple Myeloma
◽
Phase 2 Study
◽
Open Label Phase
Download Full-text
Interim safety and efficacy of a randomized (1:1), open-label phase 2 study of talimogene laherparepvec (T) and ipilimumab (I) vs I alone in unresected, stage IIIB-IV melanoma
Annals of Oncology
◽
10.1093/annonc/mdw379.04
◽
2016
◽
Vol 27
◽
pp. vi380
◽
Cited By ~ 10
Author(s):
J. Chesney
◽
F. Collichio
◽
R.H.I. Andtbacka
◽
I. Puzanov
◽
J. Glaspy
◽
...
Keyword(s):
Stage Iiib
◽
Phase 2
◽
Talimogene Laherparepvec
◽
Open Label
◽
Safety And Efficacy
◽
Phase 2 Study
◽
Open Label Phase
Download Full-text
Dasatinib as a Single Agent in Triple-Negative Breast Cancer: Results of an Open-Label Phase 2 Study
Clinical Cancer Research
◽
10.1158/1078-0432.ccr-11-0288
◽
2011
◽
Vol 17
(21)
◽
pp. 6905-6913
◽
Cited By ~ 126
Author(s):
Richard S. Finn
◽
Carmelo Bengala
◽
Nuhad Ibrahim
◽
Henri Roché
◽
Joseph Sparano
◽
...
Keyword(s):
Breast Cancer
◽
Triple Negative Breast Cancer
◽
Triple Negative
◽
Single Agent
◽
Phase 2
◽
Open Label
◽
Phase 2 Study
◽
Open Label Phase
Download Full-text
Trabectedin monotherapy after standard chemotherapy versus best supportive care in patients with advanced, translocation-related sarcoma: a randomised, open-label, phase 2 study
The Lancet Oncology
◽
10.1016/s1470-2045(15)70098-7
◽
2015
◽
Vol 16
(4)
◽
pp. 406-416
◽
Cited By ~ 97
Author(s):
Akira Kawai
◽
Nobuhito Araki
◽
Hideshi Sugiura
◽
Takafumi Ueda
◽
Tsukasa Yonemoto
◽
...
Keyword(s):
Supportive Care
◽
Best Supportive Care
◽
Phase 2
◽
Standard Chemotherapy
◽
Open Label
◽
Phase 2 Study
◽
Open Label Phase
Download Full-text
Two dosing regimens of tosedostat in elderly patients with relapsed or refractory acute myeloid leukaemia (OPAL): a randomised open-label phase 2 study
The Lancet Oncology
◽
10.1016/s1470-2045(13)70037-8
◽
2013
◽
Vol 14
(4)
◽
pp. 354-362
◽
Cited By ~ 26
Author(s):
Jorge Cortes
◽
Eric Feldman
◽
Karen Yee
◽
David Rizzieri
◽
Anjali S Advani
◽
...
Keyword(s):
Elderly Patients
◽
Acute Myeloid Leukaemia
◽
Myeloid Leukaemia
◽
Phase 2
◽
Open Label
◽
Phase 2 Study
◽
Open Label Phase
◽
Dosing Regimens
◽
Acute Myeloid
Download Full-text
The patient experience of elosulfase alfa treatment for MPS IVA (Morquio syndrome type A): beyond traditional measures
Molecular Genetics and Metabolism
◽
10.1016/j.ymgme.2016.11.165
◽
2017
◽
Vol 120
(1-2)
◽
pp. S70-S71
Author(s):
James Jarrett
◽
Mohit Jain
◽
Charlotte Roberts
◽
Alexandra Morrison
Keyword(s):
Patient Experience
◽
Type A
◽
Syndrome Type
◽
Mps Iva
◽
Morquio Syndrome
◽
Elosulfase Alfa
Download Full-text
Adjuvant docetaxel and cyclophosphamide plus trastuzumab in patients with HER2 -amplified early stage breast cancer: a single-group, open-label, phase 2 study
The Lancet Oncology
◽
10.1016/s1470-2045(13)70384-x
◽
2013
◽
Vol 14
(11)
◽
pp. 1121-1128
◽
Cited By ~ 76
Author(s):
Stephen E Jones
◽
Rufus Collea
◽
Devchand Paul
◽
Scot Sedlacek
◽
Anne M Favret
◽
...
Keyword(s):
Breast Cancer
◽
Early Stage
◽
Early Stage Breast Cancer
◽
Phase 2
◽
Single Group
◽
Open Label
◽
Phase 2 Study
◽
Open Label Phase
Download Full-text
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